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Steven J Gray

Showing results (101-110 of 107) with videos related to

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Molecular Therapy : the Journal of the American Society of Gene Therapy|November 10, 2011
Phase 1 gene therapy for Duchenne muscular dystrophy using a translational optimized AAV vectorDawn E Bowles, Scott W J McPhee, Chengwen Li, et al.
Neuroscience|May 4, 2020
Intellectual and Developmental Disabilities Research Centers: A Multidisciplinary Approach to Understand the Pathogenesis of Methyl-CpG Binding Protein 2-related DisordersMichela Fagiolini, Annarita Patrizi, Jocelyn LeBlanc, et al.
Brain : a Journal of Neurology|June 11, 2021
Giant axonal neuropathy: cross-sectional analysis of a large natural history cohortDiana X Bharucha-Goebel, Gina Norato, Dimah Saade, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|February 14, 2018
Long-Term Improvement of Neurological Signs and Metabolic Dysfunction in a Mouse Model of Krabbe's Disease after Global Gene TherapyMichael S Marshall, Yazan Issa, Benas Jakubauskas, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|May 19, 2022
Gene-based therapeutics for rare genetic neurodevelopmental psychiatric disordersBeverly L Davidson, Guangping Gao, Elizabeth Berry-Kravis, et al.
The Journal of Clinical Investigation|August 11, 2020
Krabbe disease successfully treated via monotherapy of intrathecal gene therapyAllison M Bradbury, Jessica H Bagel, Duc Nguyen, et al.
The New England Journal of Medicine|March 20, 2024
Intrathecal Gene Therapy for Giant Axonal NeuropathyDiana X Bharucha-Goebel, Joshua J Todd, Dimah Saade, et al.
Pageof 11

Showing results (101-110 of 107) with videos related to

Sort By:
Pageof 11
You have reached the last page of results.This site can display upto 107 results.
Molecular Therapy : the Journal of the American Society of Gene Therapy|November 10, 2011
Phase 1 gene therapy for Duchenne muscular dystrophy using a translational optimized AAV vectorDawn E Bowles, Scott W J McPhee, Chengwen Li, et al.
Neuroscience|May 4, 2020
Intellectual and Developmental Disabilities Research Centers: A Multidisciplinary Approach to Understand the Pathogenesis of Methyl-CpG Binding Protein 2-related DisordersMichela Fagiolini, Annarita Patrizi, Jocelyn LeBlanc, et al.
Brain : a Journal of Neurology|June 11, 2021
Giant axonal neuropathy: cross-sectional analysis of a large natural history cohortDiana X Bharucha-Goebel, Gina Norato, Dimah Saade, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|February 14, 2018
Long-Term Improvement of Neurological Signs and Metabolic Dysfunction in a Mouse Model of Krabbe's Disease after Global Gene TherapyMichael S Marshall, Yazan Issa, Benas Jakubauskas, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|May 19, 2022
Gene-based therapeutics for rare genetic neurodevelopmental psychiatric disordersBeverly L Davidson, Guangping Gao, Elizabeth Berry-Kravis, et al.
The Journal of Clinical Investigation|August 11, 2020
Krabbe disease successfully treated via monotherapy of intrathecal gene therapyAllison M Bradbury, Jessica H Bagel, Duc Nguyen, et al.
The New England Journal of Medicine|March 20, 2024
Intrathecal Gene Therapy for Giant Axonal NeuropathyDiana X Bharucha-Goebel, Joshua J Todd, Dimah Saade, et al.
Pageof 11