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Steven J Gray

Showing results (41-50 of 106) with videos related to

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Orphanet Journal of Rare Diseases|February 3, 2019
Advancing the pathologic phenotype of giant axonal neuropathy: early involvement of the ocular lensDiane Armao, Thomas W Bouldin, Rachel M Bailey, et al.
Current Protocols in Neuroscience|October 6, 2011
Production of recombinant adeno-associated viral vectors and use in in vitro and in vivo administrationSteven J Gray, Vivian W Choi, Aravind Asokan, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|November 13, 2020
Pre-clinical Gene Therapy with AAV9/AGA in Aspartylglucosaminuria Mice Provides Evidence for Clinical TranslationXin Chen, Sarah Snanoudj-Verber, Laura Pollard, et al.
Molecular Therapy. Methods & Clinical Development|December 12, 2018
Efficacy of a Bicistronic Vector for Correction of Sandhoff Disease in a Mouse ModelEvan Woodley, Karlaina J L Osmon, Patrick Thompson, et al.
American Journal of Medical Genetics. Part A|December 5, 2024
SURF1 Deficiency: Expanding on Disease Phenotype and Assessing Disease Burden by Describing Clinical and Biochemical PhenotypeSaima Kayani, Victor Daescu, Hamza Dahshi, et al.
The Journal of Clinical Investigation|January 13, 2022
AAV9/MFSD8 gene therapy is effective in preclinical models of neuronal ceroid lipofuscinosis type 7 diseaseXin Chen, Thomas Dong, Yuhui Hu, et al.
Trends in Neurosciences|February 3, 2016
Rett Syndrome: Crossing the Threshold to Clinical TranslationDavid M Katz, Adrian Bird, Monica Coenraads, et al.
Acta Neuropathologica Communications|June 17, 2017
Novel oligodendroglial alpha synuclein viral vector models of multiple system atrophy: studies in rodents and nonhuman primatesRonald J Mandel, David J Marmion, Deniz Kirik, et al.
Plos One|March 14, 2013
In cellulo examination of a beta-alpha hybrid construct of beta-hexosaminidase A subunits, reported to interact with the GM2 activator protein and hydrolyze GM2 gangliosideIncilay Sinici, Sayuri Yonekawa, Ilona Tkachyova, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|December 31, 2009
Directed evolution of a novel adeno-associated virus (AAV) vector that crosses the seizure-compromised blood-brain barrier (BBB)Steven J Gray, Bonita L Blake, Hugh E Criswell, et al.
Pageof 11

Showing results (41-50 of 106) with videos related to

Sort By:
Pageof 11
Orphanet Journal of Rare Diseases|February 3, 2019
Advancing the pathologic phenotype of giant axonal neuropathy: early involvement of the ocular lensDiane Armao, Thomas W Bouldin, Rachel M Bailey, et al.
Current Protocols in Neuroscience|October 6, 2011
Production of recombinant adeno-associated viral vectors and use in in vitro and in vivo administrationSteven J Gray, Vivian W Choi, Aravind Asokan, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|November 13, 2020
Pre-clinical Gene Therapy with AAV9/AGA in Aspartylglucosaminuria Mice Provides Evidence for Clinical TranslationXin Chen, Sarah Snanoudj-Verber, Laura Pollard, et al.
Molecular Therapy. Methods & Clinical Development|December 12, 2018
Efficacy of a Bicistronic Vector for Correction of Sandhoff Disease in a Mouse ModelEvan Woodley, Karlaina J L Osmon, Patrick Thompson, et al.
American Journal of Medical Genetics. Part A|December 5, 2024
SURF1 Deficiency: Expanding on Disease Phenotype and Assessing Disease Burden by Describing Clinical and Biochemical PhenotypeSaima Kayani, Victor Daescu, Hamza Dahshi, et al.
The Journal of Clinical Investigation|January 13, 2022
AAV9/MFSD8 gene therapy is effective in preclinical models of neuronal ceroid lipofuscinosis type 7 diseaseXin Chen, Thomas Dong, Yuhui Hu, et al.
Trends in Neurosciences|February 3, 2016
Rett Syndrome: Crossing the Threshold to Clinical TranslationDavid M Katz, Adrian Bird, Monica Coenraads, et al.
Acta Neuropathologica Communications|June 17, 2017
Novel oligodendroglial alpha synuclein viral vector models of multiple system atrophy: studies in rodents and nonhuman primatesRonald J Mandel, David J Marmion, Deniz Kirik, et al.
Plos One|March 14, 2013
In cellulo examination of a beta-alpha hybrid construct of beta-hexosaminidase A subunits, reported to interact with the GM2 activator protein and hydrolyze GM2 gangliosideIncilay Sinici, Sayuri Yonekawa, Ilona Tkachyova, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|December 31, 2009
Directed evolution of a novel adeno-associated virus (AAV) vector that crosses the seizure-compromised blood-brain barrier (BBB)Steven J Gray, Bonita L Blake, Hugh E Criswell, et al.
Pageof 11