Showing results (71-80 of 108) with videos related to
Sort By:
Pageof 11
European Journal of Haematology|March 8, 2022
Pain and functional disability amongst adults with moderate and severe haemophilia from the Irish personalised approach to the treatment of haemophilia (iPATH) studyMegan Kennedy, Brian O' Mahony, Sheila Roche, et al.Blood Advances|December 6, 2024
Long-term safety and efficacy of fitusiran prophylaxis, and perioperative management, in people with hemophilia A or BSteven W Pipe, Toshko Lissitchkov, Pencho Georgiev, et al.Molecular Therapy. Methods & Clinical Development|September 19, 2025
Natural history of preexisting AAV5 antibodies in adults with hemophilia B during the lead-in of the etranacogene dezaparvovec phase 3 studyRobert Klamroth, Michael Recht, Nigel S Key, et al.The New England Journal of Medicine|December 8, 2025
Final Analysis of a Study of Etranacogene Dezaparvovec for Hemophilia BSteven W Pipe, Wolfgang Miesbach, Michael Recht, et al.Research and Practice in Thrombosis and Haemostasis|February 3, 2025
Adeno-associated virus-based gene therapy for hemophilia-addressing the gapsWolfgang Miesbach, Paul Batty, Pratima Chowdary, et al.Blood Advances|April 6, 2025
Completion of Phase 2b trial of etranacogene dezaparvovec gene therapy in patients with hemophilia B over 5 yearsAnnette von Drygalski, Esteban Gomez, Adam Giermasz, et al.Journal of Thrombosis and Haemostasis : JTH|January 11, 2025
Accurate evaluation of factor VIII activity of efanesoctocog alfa in the presence of emicizumabChristophe Nougier, Steven W Pipe, Ingrid Pabinger, et al.The Lancet. Haematology|September 2, 2022
Achieving access to haemophilia care in low-income and lower-middle-income countries: expanded Humanitarian Aid Program of the World Federation of Hemophilia after 5 yearsGlenn F Pierce, Megan Adediran, Saliou Diop, et al.Blood|September 21, 2010
In vivo efficacy of platelet-delivered, high specific activity factor VIII variantsTeshell K Greene, Cheng Wang, Jessica D Hirsch, et al.Journal of Thrombosis and Haemostasis : JTH|October 29, 2025
A comprehensive care pathway of gene therapy for hemophilia based on current guideline documents and summary of product characteristics: communication from the ISTH SSC working group on gene therapyCaroline M A Mussert, Wolfgang Miesbach, Pratima Chowdary, et al.Pageof 11