Search research articles
Contact Us
Filters
Showing results (31-40 of 66) with videos related to
Page
of 7
Sort By:
Blood Advances
|
January 4, 2018
Gene-edited pseudogene resurrection corrects p47<sup>phox</sup>-deficient chronic granulomatous disease
Randall K Merling, Douglas B Kuhns, Colin L Sweeney, et al.
Gene Therapy
|
March 13, 2021
Correction of X-CGD patient HSPCs by targeted CYBB cDNA insertion using CRISPR/Cas9 with 53BP1 inhibition for enhanced homology-directed repair
Colin L Sweeney, Mara Pavel-Dinu, Uimook Choi, et al.
Blood Advances
|
January 18, 2019
<i>NCF1</i> (p47<sup>phox</sup>)-deficient chronic granulomatous disease: comprehensive genetic and flow cytometric analysis
Douglas B Kuhns, Amy P Hsu, David Sun, et al.
Biorxiv : the Preprint Server for Biology
|
June 26, 2025
A novel frameshift mutation in Phosphoinositide 3-kinase regulatory subunit 1 (<i>PIK3R1</i>) causes immunodeficiency and Amyotrophic Lateral Sclerosis (ALS)
Brice Calco, Colin L Sweeney, Joseph Steiner, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
October 8, 2014
An AAVS1-targeted minigene platform for correction of iPSCs from all five types of chronic granulomatous disease
Randall K Merling, Colin L Sweeney, Jessica Chu, et al.
Cytotherapy
|
October 14, 2020
MAGT1 messenger RNA-corrected autologous T and natural killer cells for potential cell therapy in X-linked immunodeficiency with magnesium defect, Epstein-Barr virus infection and neoplasia disease
Julie Brault, Ronald J Meis, Linhong Li, et al.
Blood
|
October 18, 2012
Humans with chronic granulomatous disease maintain humoral immunologic memory despite low frequencies of circulating memory B cells
Susan Moir, Suk See De Ravin, Brian H Santich, et al.
Clinical Infectious Diseases : an Official Publication of the Infectious Diseases Society of America
|
March 4, 2011
Geosmithia argillacea: an emerging cause of invasive mycosis in human chronic granulomatous disease
Suk See De Ravin, Malliswari Challipalli, Victoria Anderson, et al.
Blood
|
July 10, 2010
Severe congenital neutropenia resulting from G6PC3 deficiency with increased neutrophil CXCR4 expression and myelokathexis
David H McDermott, Suk See De Ravin, Hyun Sik Jun, et al.
Science Translational Medicine
|
January 13, 2017
CRISPR-Cas9 gene repair of hematopoietic stem cells from patients with X-linked chronic granulomatous disease
Suk See De Ravin, Linhong Li, Xiaolin Wu, et al.
Page
of 7
Search research articles
Search
Showing results (31-40 of 66) with videos related to
Sort By:
Page
of 7
Blood Advances
|
January 4, 2018
Gene-edited pseudogene resurrection corrects p47<sup>phox</sup>-deficient chronic granulomatous disease
Randall K Merling, Douglas B Kuhns, Colin L Sweeney, et al.
Gene Therapy
|
March 13, 2021
Correction of X-CGD patient HSPCs by targeted CYBB cDNA insertion using CRISPR/Cas9 with 53BP1 inhibition for enhanced homology-directed repair
Colin L Sweeney, Mara Pavel-Dinu, Uimook Choi, et al.
Blood Advances
|
January 18, 2019
<i>NCF1</i> (p47<sup>phox</sup>)-deficient chronic granulomatous disease: comprehensive genetic and flow cytometric analysis
Douglas B Kuhns, Amy P Hsu, David Sun, et al.
Biorxiv : the Preprint Server for Biology
|
June 26, 2025
A novel frameshift mutation in Phosphoinositide 3-kinase regulatory subunit 1 (<i>PIK3R1</i>) causes immunodeficiency and Amyotrophic Lateral Sclerosis (ALS)
Brice Calco, Colin L Sweeney, Joseph Steiner, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
October 8, 2014
An AAVS1-targeted minigene platform for correction of iPSCs from all five types of chronic granulomatous disease
Randall K Merling, Colin L Sweeney, Jessica Chu, et al.
Cytotherapy
|
October 14, 2020
MAGT1 messenger RNA-corrected autologous T and natural killer cells for potential cell therapy in X-linked immunodeficiency with magnesium defect, Epstein-Barr virus infection and neoplasia disease
Julie Brault, Ronald J Meis, Linhong Li, et al.
Blood
|
October 18, 2012
Humans with chronic granulomatous disease maintain humoral immunologic memory despite low frequencies of circulating memory B cells
Susan Moir, Suk See De Ravin, Brian H Santich, et al.
Clinical Infectious Diseases : an Official Publication of the Infectious Diseases Society of America
|
March 4, 2011
Geosmithia argillacea: an emerging cause of invasive mycosis in human chronic granulomatous disease
Suk See De Ravin, Malliswari Challipalli, Victoria Anderson, et al.
Blood
|
July 10, 2010
Severe congenital neutropenia resulting from G6PC3 deficiency with increased neutrophil CXCR4 expression and myelokathexis
David H McDermott, Suk See De Ravin, Hyun Sik Jun, et al.
Science Translational Medicine
|
January 13, 2017
CRISPR-Cas9 gene repair of hematopoietic stem cells from patients with X-linked chronic granulomatous disease
Suk See De Ravin, Linhong Li, Xiaolin Wu, et al.
Page
of 7