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Seizure
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August 27, 2025
Cerliponase alfa therapy leads to long-term seizure freedom in a patient with late infantile neuronal ceroid lipofuscinosis
Anita N Datta, Sylvia Stockler
The Tohoku Journal of Experimental Medicine
|
January 5, 2007
Cerebral folate deficiency and folinic acid treatment in hypomyelination with atrophy of the basal ganglia and cerebellum (H-ABC) syndrome
Saadet Mercimek-Mahmutoglu, Sylvia Stockler-Ipsiroglu
International Journal of Molecular Sciences
|
December 3, 2020
Morquio B Disease. Disease Characteristics and Treatment Options of a Distinct <i>GLB1</i>-Related Dysostosis Multiplex
Nataliya Yuskiv, Katsumi Higaki, Sylvia Stockler-Ipsiroglu
Molecular Genetics and Metabolism
|
January 4, 2012
Treatable inborn errors of metabolism causing intellectual disability: a systematic literature review
Clara D M van Karnebeek, Sylvia Stockler
Paediatrics & Child Health
|
November 22, 2014
Early identification of treatable inborn errors of metabolism in children with intellectual disability: The Treatable Intellectual Disability Endeavor protocol in British Columbia
Clara Dm van Karnebeek, Sylvia Stockler-Ipsiroglu
Seminars in Neurology
|
September 6, 2014
Cerebral creatine deficiencies: a group of treatable intellectual developmental disorders
Sylvia Stockler-Ipsiroglu, Clara D M van Karnebeek
Frontiers in Pediatrics
|
March 19, 2024
Morquio B disease: a case report
Tara Gholamian, Harpreet Chhina, Sylvia Stockler, et al.
Sub-Cellular Biochemistry
|
July 26, 2008
Cerebral creatine deficiency syndromes: clinical aspects, treatment and pathophysiology
Sylvia Stockler, Peter W Schutz, Gajja S Salomons
Paediatrics & Child Health
|
October 22, 2021
Diagnostic yield from routine metabolic screening tests in evaluation of global developmental delay and intellectual disability
Hilary Vallance, Graham Sinclair, Bojana Rakic, et al.
Molecular Genetics and Metabolism
|
December 31, 2021
Determining ideal balance among branched-chain amino acids in medical formula for Propionic Acidemia: A proof of concept study in healthy children
Haneen Saleemani, Gabriella Horvath, Sylvia Stockler-Ipsiroglu, et al.
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Search research articles
Search
Showing results (1-10 of 125) with videos related to
Sort By:
Page
of 13
Seizure
|
August 27, 2025
Cerliponase alfa therapy leads to long-term seizure freedom in a patient with late infantile neuronal ceroid lipofuscinosis
Anita N Datta, Sylvia Stockler
The Tohoku Journal of Experimental Medicine
|
January 5, 2007
Cerebral folate deficiency and folinic acid treatment in hypomyelination with atrophy of the basal ganglia and cerebellum (H-ABC) syndrome
Saadet Mercimek-Mahmutoglu, Sylvia Stockler-Ipsiroglu
International Journal of Molecular Sciences
|
December 3, 2020
Morquio B Disease. Disease Characteristics and Treatment Options of a Distinct <i>GLB1</i>-Related Dysostosis Multiplex
Nataliya Yuskiv, Katsumi Higaki, Sylvia Stockler-Ipsiroglu
Molecular Genetics and Metabolism
|
January 4, 2012
Treatable inborn errors of metabolism causing intellectual disability: a systematic literature review
Clara D M van Karnebeek, Sylvia Stockler
Paediatrics & Child Health
|
November 22, 2014
Early identification of treatable inborn errors of metabolism in children with intellectual disability: The Treatable Intellectual Disability Endeavor protocol in British Columbia
Clara Dm van Karnebeek, Sylvia Stockler-Ipsiroglu
Seminars in Neurology
|
September 6, 2014
Cerebral creatine deficiencies: a group of treatable intellectual developmental disorders
Sylvia Stockler-Ipsiroglu, Clara D M van Karnebeek
Frontiers in Pediatrics
|
March 19, 2024
Morquio B disease: a case report
Tara Gholamian, Harpreet Chhina, Sylvia Stockler, et al.
Sub-Cellular Biochemistry
|
July 26, 2008
Cerebral creatine deficiency syndromes: clinical aspects, treatment and pathophysiology
Sylvia Stockler, Peter W Schutz, Gajja S Salomons
Paediatrics & Child Health
|
October 22, 2021
Diagnostic yield from routine metabolic screening tests in evaluation of global developmental delay and intellectual disability
Hilary Vallance, Graham Sinclair, Bojana Rakic, et al.
Molecular Genetics and Metabolism
|
December 31, 2021
Determining ideal balance among branched-chain amino acids in medical formula for Propionic Acidemia: A proof of concept study in healthy children
Haneen Saleemani, Gabriella Horvath, Sylvia Stockler-Ipsiroglu, et al.
Page
of 13