Showing results (1-10 of 23) with videos related to
Sort By:
Pageof 3
Therapeutics and Clinical Risk Management|October 22, 2019
Clinical Evidence Supporting Early Treatment Of Patients With Spinal Muscular Atrophy: Current PerspectivesTamara Dangouloff, Laurent ServaisNeuromuscular Disorders : NMD|October 8, 2021
Newborn screening of neuromuscular diseasesTamara Dangouloff, François Boemer, Laurent ServaisJournal of Neuromuscular Diseases|February 20, 2025
Newborn screening programs for spinal muscular atrophy worldwide in 2023Eva Vrščaj, Tamara Dangouloff, Damjan Osredkar, et al.Neuromuscular Disorders : NMD|May 14, 2021
Newborn screening programs for spinal muscular atrophy worldwide: Where we stand and where to goTamara Dangouloff, Eva Vrščaj, Laurent Servais, et al.Journal of Neuromuscular Diseases|February 20, 2025
Newborn screening and rapid genomic diagnosis of neuromuscular diseasesTamara Dangouloff, Helena Lang, Noor Benmhammed, et al.Genes|July 29, 2023
Spinal Muscular Atrophy Treatment in Patients Identified by Newborn Screening-A Systematic ReviewKarolina Aragon-Gawinska, Charlotte Mouraux, Tamara Dangouloff, et al.Neuromuscular Disorders : NMD|December 29, 2019
244th ENMC international workshop: Newborn screening in spinal muscular atrophy May 10-12, 2019, Hoofdorp, The NetherlandsTamara Dangouloff, Arthur Burghes, Eduardo F Tizzano, et al.Orphanet Journal of Rare Diseases|January 24, 2021
Systematic literature review of the economic burden of spinal muscular atrophy and economic evaluations of treatmentsTamara Dangouloff, Camille Botty, Charlotte Beaudart, et al.Developmental Medicine and Child Neurology|June 8, 2022
Financial cost and quality of life of patients with spinal muscular atrophy identified by symptoms or newborn screeningTamara Dangouloff, Mickael Hiligsmann, Nicolas Deconinck, et al.Molecular Therapy. Advances|May 15, 2026
Elective preterm birth for earlier spinal muscular atrophy treatmentTamara Dangouloff, Frédéric Chantraine, Nadège Hennuy, et al.Pageof 3