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Molecular Therapy : the Journal of the American Society of Gene Therapy
|
January 14, 2024
Missense suppressor tRNA therapeutics correct disease-causing alleles by misreading the genetic code
Teija M I Bily, Ilka U Heinemann, Patrick O'Donoghue
RNA (New York, N.Y.)
|
March 21, 2025
Natural human tRNA<sup>Ala</sup> anticodon variants mistranslate the genetic code
Rasangi Tennakoon, Teija M I Bily, Farah Hasan, et al.
Genome Research
|
November 23, 2019
Modeling Niemann-Pick disease type C in a human haploid cell line allows for patient variant characterization and clinical interpretation
Steven Erwood, Reid A Brewer, Teija M I Bily, et al.
Molecular Therapy. Nucleic Acids
|
February 3, 2025
Glutamine missense suppressor transfer RNAs inhibit polyglutamine aggregation
Rasangi Tennakoon, Teija M I Bily, Farah Hasan, et al.
Molecular Therapy. Methods & Clinical Development
|
June 4, 2020
Allele-Specific Prevention of Nonsense-Mediated Decay in Cystic Fibrosis Using Homology-Independent Genome Editing
Steven Erwood, Onofrio Laselva, Teija M I Bily, et al.
Nature Biotechnology
|
February 22, 2022
Saturation variant interpretation using CRISPR prime editing
Steven Erwood, Teija M I Bily, Jason Lequyer, et al.
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Search research articles
Search
Showing results (1-10 of 6) with videos related to
Sort By:
Page
of 1
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
January 14, 2024
Missense suppressor tRNA therapeutics correct disease-causing alleles by misreading the genetic code
Teija M I Bily, Ilka U Heinemann, Patrick O'Donoghue
RNA (New York, N.Y.)
|
March 21, 2025
Natural human tRNA<sup>Ala</sup> anticodon variants mistranslate the genetic code
Rasangi Tennakoon, Teija M I Bily, Farah Hasan, et al.
Genome Research
|
November 23, 2019
Modeling Niemann-Pick disease type C in a human haploid cell line allows for patient variant characterization and clinical interpretation
Steven Erwood, Reid A Brewer, Teija M I Bily, et al.
Molecular Therapy. Nucleic Acids
|
February 3, 2025
Glutamine missense suppressor transfer RNAs inhibit polyglutamine aggregation
Rasangi Tennakoon, Teija M I Bily, Farah Hasan, et al.
Molecular Therapy. Methods & Clinical Development
|
June 4, 2020
Allele-Specific Prevention of Nonsense-Mediated Decay in Cystic Fibrosis Using Homology-Independent Genome Editing
Steven Erwood, Onofrio Laselva, Teija M I Bily, et al.
Nature Biotechnology
|
February 22, 2022
Saturation variant interpretation using CRISPR prime editing
Steven Erwood, Teija M I Bily, Jason Lequyer, et al.
Page
of 1