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Thomas Gaj

Showing results (41-50 of 53) with videos related to

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Biorxiv : the Preprint Server for Biology|January 3, 2024
A high-fidelity CRISPR-Cas13 system improves abnormalities associated with C9ORF72-linked ALS/FTDTristan X McCallister, Colin K W Lim, William M Terpstra, et al.
Science Advances|January 19, 2022
Targeted gene silencing in the nervous system with CRISPR-Cas13Jackson E Powell, Colin K W Lim, Ramya Krishnan, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|January 29, 2020
Treatment of a Mouse Model of ALS by In Vivo Base EditingColin K W Lim, Michael Gapinske, Alexandra K Brooks, et al.
Stem Cell Reports|April 10, 2018
hPSC-Derived Striatal Cells Generated Using a Scalable 3D Hydrogel Promote Recovery in a Huntington Disease Mouse ModelMaroof M Adil, Thomas Gaj, Antara T Rao, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|August 15, 2022
CRISPR base editing of cis-regulatory elements enables the perturbation of neurodegeneration-linked genesColin K W Lim, Tristan X McCallister, Christian Saporito-Magriña, et al.
Nature Communications|November 28, 2024
SPLICER: a highly efficient base editing toolbox that enables in vivo therapeutic exon skippingAngelo Miskalis, Shraddha Shirguppe, Jackson Winter, et al.
Biorxiv : the Preprint Server for Biology|June 17, 2024
SPLICER: A Highly Efficient Base Editing Toolbox That Enables <i>In Vivo</i> Therapeutic Exon SkippingAngelo Miskalis, Shraddha Shirguppe, Jackson Winter, et al.
Nature Communications|January 8, 2025
A high-fidelity CRISPR-Cas13 system improves abnormalities associated with C9ORF72-linked ALS/FTDTristan X McCallister, Colin K W Lim, Mayuri Singh, et al.
Stem Cell Reports|May 30, 2017
Defined and Scalable Differentiation of Human Oligodendrocyte Precursors from Pluripotent Stem Cells in a 3D Culture SystemGonçalo M C Rodrigues, Thomas Gaj, Maroof M Adil, et al.
Biorxiv : the Preprint Server for Biology|July 15, 2024
In vivo CRISPR base editing for treatment of Huntington's diseaseShraddha Shirguppe, Michael Gapinske, Devyani Swami, et al.
Pageof 6

Showing results (41-50 of 53) with videos related to

Sort By:
Pageof 6
Biorxiv : the Preprint Server for Biology|January 3, 2024
A high-fidelity CRISPR-Cas13 system improves abnormalities associated with C9ORF72-linked ALS/FTDTristan X McCallister, Colin K W Lim, William M Terpstra, et al.
Science Advances|January 19, 2022
Targeted gene silencing in the nervous system with CRISPR-Cas13Jackson E Powell, Colin K W Lim, Ramya Krishnan, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|January 29, 2020
Treatment of a Mouse Model of ALS by In Vivo Base EditingColin K W Lim, Michael Gapinske, Alexandra K Brooks, et al.
Stem Cell Reports|April 10, 2018
hPSC-Derived Striatal Cells Generated Using a Scalable 3D Hydrogel Promote Recovery in a Huntington Disease Mouse ModelMaroof M Adil, Thomas Gaj, Antara T Rao, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|August 15, 2022
CRISPR base editing of cis-regulatory elements enables the perturbation of neurodegeneration-linked genesColin K W Lim, Tristan X McCallister, Christian Saporito-Magriña, et al.
Nature Communications|November 28, 2024
SPLICER: a highly efficient base editing toolbox that enables in vivo therapeutic exon skippingAngelo Miskalis, Shraddha Shirguppe, Jackson Winter, et al.
Biorxiv : the Preprint Server for Biology|June 17, 2024
SPLICER: A Highly Efficient Base Editing Toolbox That Enables <i>In Vivo</i> Therapeutic Exon SkippingAngelo Miskalis, Shraddha Shirguppe, Jackson Winter, et al.
Nature Communications|January 8, 2025
A high-fidelity CRISPR-Cas13 system improves abnormalities associated with C9ORF72-linked ALS/FTDTristan X McCallister, Colin K W Lim, Mayuri Singh, et al.
Stem Cell Reports|May 30, 2017
Defined and Scalable Differentiation of Human Oligodendrocyte Precursors from Pluripotent Stem Cells in a 3D Culture SystemGonçalo M C Rodrigues, Thomas Gaj, Maroof M Adil, et al.
Biorxiv : the Preprint Server for Biology|July 15, 2024
In vivo CRISPR base editing for treatment of Huntington's diseaseShraddha Shirguppe, Michael Gapinske, Devyani Swami, et al.
Pageof 6