Search research articles
Contact Us
Filters
Showing results (31-40 of 42) with videos related to
Page
of 5
Sort By:
Human Gene Therapy
|
July 9, 2009
Human RPE65 gene therapy for Leber congenital amaurosis: persistence of early visual improvements and safety at 1 year
Artur V Cideciyan, William W Hauswirth, Tomas S Aleman, et al.
Genetic Vaccines and Therapy
|
June 20, 2012
An acidic oligopeptide displayed on AAV2 improves axial muscle tropism after systemic delivery
Ni-Chung Lee, Darin J Falk, Barry J Byrne, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
January 28, 2010
Gel-mediated delivery of AAV1 vectors corrects ventilatory function in Pompe mice with established disease
Cathryn S Mah, Darin J Falk, Sean A Germain, et al.
Human Gene Therapy
|
August 1, 2012
The human rhodopsin kinase promoter in an AAV5 vector confers rod- and cone-specific expression in the primate retina
Shannon E Boye, John J Alexander, Sanford L Boye, et al.
Nature Communications
|
November 28, 2025
Gene therapy delivery of anti-Müllerian hormone in prepubertal female domestic cats induces long-term sterilization
Philippe Godin, Nicholas Nagykery, Natalie Sicher, et al.
Human Gene Therapy. Clinical Development
|
May 23, 2013
Preclinical potency and safety studies of an AAV2-mediated gene therapy vector for the treatment of MERTK associated retinitis pigmentosa
Thomas J Conlon, Wen-Tao Deng, Kirsten Erger, et al.
Human Gene Therapy. Clinical Development
|
October 4, 2018
Toxicology and Pharmacology of an AAV Vector Expressing Codon-Optimized RPGR in RPGR-Deficient Rd9 Mice
Chunjuan Song, Thomas J Conlon, Wen-Tao Deng, et al.
Human Gene Therapy
|
September 1, 2006
Safety in nonhuman primates of ocular AAV2-RPE65, a candidate treatment for blindness in Leber congenital amaurosis
Samuel G Jacobson, Sanford L Boye, Tomas S Aleman, et al.
Human Molecular Genetics
|
April 27, 2011
Pompe disease gene therapy
Barry J Byrne, Darin J Falk, Christina A Pacak, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
April 29, 2006
Safety of recombinant adeno-associated virus type 2-RPE65 vector delivered by ocular subretinal injection
Samuel G Jacobson, Gregory M Acland, Gustavo D Aguirre, et al.
Page
of 5
Search research articles
Search
Showing results (31-40 of 42) with videos related to
Sort By:
Page
of 5
Human Gene Therapy
|
July 9, 2009
Human RPE65 gene therapy for Leber congenital amaurosis: persistence of early visual improvements and safety at 1 year
Artur V Cideciyan, William W Hauswirth, Tomas S Aleman, et al.
Genetic Vaccines and Therapy
|
June 20, 2012
An acidic oligopeptide displayed on AAV2 improves axial muscle tropism after systemic delivery
Ni-Chung Lee, Darin J Falk, Barry J Byrne, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
January 28, 2010
Gel-mediated delivery of AAV1 vectors corrects ventilatory function in Pompe mice with established disease
Cathryn S Mah, Darin J Falk, Sean A Germain, et al.
Human Gene Therapy
|
August 1, 2012
The human rhodopsin kinase promoter in an AAV5 vector confers rod- and cone-specific expression in the primate retina
Shannon E Boye, John J Alexander, Sanford L Boye, et al.
Nature Communications
|
November 28, 2025
Gene therapy delivery of anti-Müllerian hormone in prepubertal female domestic cats induces long-term sterilization
Philippe Godin, Nicholas Nagykery, Natalie Sicher, et al.
Human Gene Therapy. Clinical Development
|
May 23, 2013
Preclinical potency and safety studies of an AAV2-mediated gene therapy vector for the treatment of MERTK associated retinitis pigmentosa
Thomas J Conlon, Wen-Tao Deng, Kirsten Erger, et al.
Human Gene Therapy. Clinical Development
|
October 4, 2018
Toxicology and Pharmacology of an AAV Vector Expressing Codon-Optimized RPGR in RPGR-Deficient Rd9 Mice
Chunjuan Song, Thomas J Conlon, Wen-Tao Deng, et al.
Human Gene Therapy
|
September 1, 2006
Safety in nonhuman primates of ocular AAV2-RPE65, a candidate treatment for blindness in Leber congenital amaurosis
Samuel G Jacobson, Sanford L Boye, Tomas S Aleman, et al.
Human Molecular Genetics
|
April 27, 2011
Pompe disease gene therapy
Barry J Byrne, Darin J Falk, Christina A Pacak, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
April 29, 2006
Safety of recombinant adeno-associated virus type 2-RPE65 vector delivered by ocular subretinal injection
Samuel G Jacobson, Gregory M Acland, Gustavo D Aguirre, et al.
Page
of 5