Search research articles
Contact Us
Filters
Showing results (71-80 of 95) with videos related to
Page
of 10
Sort By:
Scientific Reports
|
November 9, 2017
Urinary sulphatoxymelatonin as a biomarker of serotonin status in biogenic amine-deficient patients
Marta Batllori, Marta Molero-Luis, Luisa Arrabal, et al.
Journal of Inherited Metabolic Disease
|
November 11, 2025
Consensus Guideline for the Diagnosis and Treatment of Tyrosine Hydroxylase (TH) Deficiency
Mariya Sigatullina Bondarenko, Oya Kuseyri Hübschmann, Jan Kulhánek, et al.
Movement Disorders : Official Journal of the Movement Disorder Society
|
November 5, 2020
Novel Protein Biomarkers of Monoamine Metabolism Defects Correlate with Disease Severity
Alba Tristán-Noguero, Eva Borràs, Marta Molero-Luis, et al.
Orphanet Journal of Rare Diseases
|
January 20, 2017
Consensus guideline for the diagnosis and treatment of aromatic l-amino acid decarboxylase (AADC) deficiency
Tessa Wassenberg, Marta Molero-Luis, Kathrin Jeltsch, et al.
Journal of Inherited Metabolic Disease
|
November 18, 2016
Proposed recommendations for diagnosing and managing individuals with glutaric aciduria type I: second revision
Nikolas Boy, Chris Mühlhausen, Esther M Maier, et al.
Journal of Inherited Metabolic Disease
|
May 6, 2020
AADC deficiency from infancy to adulthood: Symptoms and developmental outcome in an international cohort of 63 patients
Toni S Pearson, Laura Gilbert, Thomas Opladen, et al.
Annals of Neurology
|
May 26, 2022
Integrative Approach to Predict Severity in Nonketotic Hyperglycinemia
Oya Kuseyri Hübschmann, Natalia Alexandra Juliá-Palacios, Mireia Olivella, et al.
Movement Disorders : Official Journal of the Movement Disorder Society
|
March 15, 2025
Patients with Allan-Herndon-Dudley Syndrome (MCT8 Deficiency) Display Symptoms of Parkinsonism in Childhood and Respond to Levodopa/Carbidopa Treatment
Nina-Maria Wilpert, Angela L Hewitt, Roser Pons, et al.
Neuroradiology
|
June 6, 2022
Volumetric study of brain MRI in a cohort of patients with neurotransmitter disorders
Chiara Alfonsi, Christian Stephan-Otto, Elisenda Cortès-Saladelafont, et al.
Journal of Inherited Metabolic Disease
|
March 19, 2024
The continuously evolving phenotype of succinic semialdehyde dehydrogenase deficiency
Natalia Alexandra Julia-Palacios, Oya Kuseyri Hübschmann, Mireia Olivella, et al.
Page
of 10
Search research articles
Search
Showing results (71-80 of 95) with videos related to
Sort By:
Page
of 10
Scientific Reports
|
November 9, 2017
Urinary sulphatoxymelatonin as a biomarker of serotonin status in biogenic amine-deficient patients
Marta Batllori, Marta Molero-Luis, Luisa Arrabal, et al.
Journal of Inherited Metabolic Disease
|
November 11, 2025
Consensus Guideline for the Diagnosis and Treatment of Tyrosine Hydroxylase (TH) Deficiency
Mariya Sigatullina Bondarenko, Oya Kuseyri Hübschmann, Jan Kulhánek, et al.
Movement Disorders : Official Journal of the Movement Disorder Society
|
November 5, 2020
Novel Protein Biomarkers of Monoamine Metabolism Defects Correlate with Disease Severity
Alba Tristán-Noguero, Eva Borràs, Marta Molero-Luis, et al.
Orphanet Journal of Rare Diseases
|
January 20, 2017
Consensus guideline for the diagnosis and treatment of aromatic l-amino acid decarboxylase (AADC) deficiency
Tessa Wassenberg, Marta Molero-Luis, Kathrin Jeltsch, et al.
Journal of Inherited Metabolic Disease
|
November 18, 2016
Proposed recommendations for diagnosing and managing individuals with glutaric aciduria type I: second revision
Nikolas Boy, Chris Mühlhausen, Esther M Maier, et al.
Journal of Inherited Metabolic Disease
|
May 6, 2020
AADC deficiency from infancy to adulthood: Symptoms and developmental outcome in an international cohort of 63 patients
Toni S Pearson, Laura Gilbert, Thomas Opladen, et al.
Annals of Neurology
|
May 26, 2022
Integrative Approach to Predict Severity in Nonketotic Hyperglycinemia
Oya Kuseyri Hübschmann, Natalia Alexandra Juliá-Palacios, Mireia Olivella, et al.
Movement Disorders : Official Journal of the Movement Disorder Society
|
March 15, 2025
Patients with Allan-Herndon-Dudley Syndrome (MCT8 Deficiency) Display Symptoms of Parkinsonism in Childhood and Respond to Levodopa/Carbidopa Treatment
Nina-Maria Wilpert, Angela L Hewitt, Roser Pons, et al.
Neuroradiology
|
June 6, 2022
Volumetric study of brain MRI in a cohort of patients with neurotransmitter disorders
Chiara Alfonsi, Christian Stephan-Otto, Elisenda Cortès-Saladelafont, et al.
Journal of Inherited Metabolic Disease
|
March 19, 2024
The continuously evolving phenotype of succinic semialdehyde dehydrogenase deficiency
Natalia Alexandra Julia-Palacios, Oya Kuseyri Hübschmann, Mireia Olivella, et al.
Page
of 10