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Nucleic Acid Therapeutics
|
February 10, 2021
Splice-Switching Antisense Oligonucleotides as a Targeted Intrinsic Engineering Tool for Generating Armored Redirected T Cells
Erica Ceccarello, Tommaso Tabaglio, Sarene Koh, et al.
Chemical Communications (Cambridge, England)
|
September 23, 2024
A splice-switch oligonucleotide loaded self-cleavable DNA nanogel
Yuwei Hu, Feng Chen, Hongfang Lu, et al.
Science Signaling
|
April 4, 2019
Proteomics profiling of arginine methylation defines PRMT5 substrate specificity
Daniele Musiani, Jabez Bok, Enrico Massignani, et al.
Journal of Cell Science
|
September 22, 2025
Differential splice isoforms of mouse CDK2 play functionally redundant roles during mitotic and meiotic division
Nathan Palmer, Nisan Ece Kalem-Yapar, Hanna Hultén, et al.
Life Science Alliance
|
November 21, 2018
MBNL1 alternative splicing isoforms play opposing roles in cancer
Tommaso Tabaglio, Diana Hp Low, Winnie Koon Lay Teo, et al.
Molecular Therapy. Nucleic Acids
|
February 10, 2025
Unveiling sequence-agnostic mixed-chemical modification patterns for splice-switching oligonucleotides using the NATURA platform
Tommaso Tabaglio, Taniya Agarwal, Wei Yuan Cher, et al.
Human Molecular Genetics
|
August 1, 2014
Functional variations modulating PRKCA expression and alternative splicing predispose to multiple sclerosis
Elvezia M Paraboschi, Valeria Rimoldi, Giulia Soldà, et al.
Cancer Cell
|
January 15, 2020
Epigenetic Silencing of CDR1as Drives IGF2BP3-Mediated Melanoma Invasion and Metastasis
Douglas Hanniford, Alejandro Ulloa-Morales, Alcida Karz, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
December 12, 2025
BLOC1S1 depletion via splice-switching oligonucleotides improves mitochondrial respiration and rescues ALS phenotypes
Jin-Hui Hor, Jin Rong Ow, Winanto Ng, et al.
Nature Communications
|
February 2, 2023
G9a/GLP inhibition during ex vivo lymphocyte expansion increases in vivo cytotoxicity of engineered T cells against hepatocellular carcinoma
Maxine S Y Lam, Jose Antonio Reales-Calderon, Jin Rong Ow, et al.
Page
of 2
Search research articles
Search
Showing results (1-10 of 18) with videos related to
Sort By:
Page
of 2
Nucleic Acid Therapeutics
|
February 10, 2021
Splice-Switching Antisense Oligonucleotides as a Targeted Intrinsic Engineering Tool for Generating Armored Redirected T Cells
Erica Ceccarello, Tommaso Tabaglio, Sarene Koh, et al.
Chemical Communications (Cambridge, England)
|
September 23, 2024
A splice-switch oligonucleotide loaded self-cleavable DNA nanogel
Yuwei Hu, Feng Chen, Hongfang Lu, et al.
Science Signaling
|
April 4, 2019
Proteomics profiling of arginine methylation defines PRMT5 substrate specificity
Daniele Musiani, Jabez Bok, Enrico Massignani, et al.
Journal of Cell Science
|
September 22, 2025
Differential splice isoforms of mouse CDK2 play functionally redundant roles during mitotic and meiotic division
Nathan Palmer, Nisan Ece Kalem-Yapar, Hanna Hultén, et al.
Life Science Alliance
|
November 21, 2018
MBNL1 alternative splicing isoforms play opposing roles in cancer
Tommaso Tabaglio, Diana Hp Low, Winnie Koon Lay Teo, et al.
Molecular Therapy. Nucleic Acids
|
February 10, 2025
Unveiling sequence-agnostic mixed-chemical modification patterns for splice-switching oligonucleotides using the NATURA platform
Tommaso Tabaglio, Taniya Agarwal, Wei Yuan Cher, et al.
Human Molecular Genetics
|
August 1, 2014
Functional variations modulating PRKCA expression and alternative splicing predispose to multiple sclerosis
Elvezia M Paraboschi, Valeria Rimoldi, Giulia Soldà, et al.
Cancer Cell
|
January 15, 2020
Epigenetic Silencing of CDR1as Drives IGF2BP3-Mediated Melanoma Invasion and Metastasis
Douglas Hanniford, Alejandro Ulloa-Morales, Alcida Karz, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
December 12, 2025
BLOC1S1 depletion via splice-switching oligonucleotides improves mitochondrial respiration and rescues ALS phenotypes
Jin-Hui Hor, Jin Rong Ow, Winanto Ng, et al.
Nature Communications
|
February 2, 2023
G9a/GLP inhibition during ex vivo lymphocyte expansion increases in vivo cytotoxicity of engineered T cells against hepatocellular carcinoma
Maxine S Y Lam, Jose Antonio Reales-Calderon, Jin Rong Ow, et al.
Page
of 2