Search research articles
Contact Us
Filters
Showing results (121-130 of 172) with videos related to
Page
of 18
Sort By:
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
April 1, 2024
CRISPR-Cas9n-mediated ELANE promoter editing for gene therapy of severe congenital neutropenia
Masoud Nasri, Malte U Ritter, Perihan Mir, et al.
Nature Communications
|
January 3, 2024
Transient inhibition of 53BP1 increases the frequency of targeted integration in human hematopoietic stem and progenitor cells
Ron Baik, M Kyle Cromer, Steve E Glenn, et al.
Molecular Therapy. Methods & Clinical Development
|
March 26, 2021
Anti-CD19 CARs displayed at the surface of lentiviral vector particles promote transduction of target-expressing cells
Nicole Cordes, Carolin Kolbe, Dominik Lock, et al.
Communications Biology
|
October 9, 2024
Gene editing of NCF1 loci is associated with homologous recombination and chromosomal rearrangements
Federica Raimondi, Kah Mun Siow, Dominik Wrona, et al.
Molecular Therapy. Nucleic Acids
|
August 30, 2021
A non-viral and selection-free <i>COL7A1</i> HDR approach with improved safety profile for dystrophic epidermolysis bullosa
Thomas Kocher, Johannes Bischof, Simone Alexandra Haas, et al.
Frontiers in Immunology
|
March 4, 2024
Artificial Targets: a versatile cell-free platform to characterize CAR T cell function <i>in vitro</i>
Xueting Wang, Nicholas J A Tokarew, Nadine Borgelt, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
November 19, 2025
Base edited skin equivalents with clinical potential for ex vivo correction of recessive dystrophic epidermolysis bullosa
Alex Bassons-Bascuñana, Blanca Duarte, Estela Méndez-Jiménez, et al.
Nature Communications
|
May 8, 2026
Simultaneous orthogonal cell engineering by a single CRISPR-Cas9 polyfunctional editor
Deborah Cipria, Tania Baccega, Miriana Rizzo, et al.
Nucleic Acids Research
|
April 29, 2025
Donor insertion into CX3CR1 allows epigenetic modulation of a constitutive promoter on hematopoietic stem cells and its activation upon myeloid differentiation
Iris Ramos-Hernández, Carla Fuster-García, Araceli Aguilar-González, et al.
Nature Methods
|
September 23, 2024
Effective genome editing with an enhanced ISDra2 TnpB system and deep learning-predicted ωRNAs
Kim Fabiano Marquart, Nicolas Mathis, Amina Mollaysa, et al.
Page
of 18
Search research articles
Search
Showing results (121-130 of 172) with videos related to
Sort By:
Page
of 18
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
April 1, 2024
CRISPR-Cas9n-mediated ELANE promoter editing for gene therapy of severe congenital neutropenia
Masoud Nasri, Malte U Ritter, Perihan Mir, et al.
Nature Communications
|
January 3, 2024
Transient inhibition of 53BP1 increases the frequency of targeted integration in human hematopoietic stem and progenitor cells
Ron Baik, M Kyle Cromer, Steve E Glenn, et al.
Molecular Therapy. Methods & Clinical Development
|
March 26, 2021
Anti-CD19 CARs displayed at the surface of lentiviral vector particles promote transduction of target-expressing cells
Nicole Cordes, Carolin Kolbe, Dominik Lock, et al.
Communications Biology
|
October 9, 2024
Gene editing of NCF1 loci is associated with homologous recombination and chromosomal rearrangements
Federica Raimondi, Kah Mun Siow, Dominik Wrona, et al.
Molecular Therapy. Nucleic Acids
|
August 30, 2021
A non-viral and selection-free <i>COL7A1</i> HDR approach with improved safety profile for dystrophic epidermolysis bullosa
Thomas Kocher, Johannes Bischof, Simone Alexandra Haas, et al.
Frontiers in Immunology
|
March 4, 2024
Artificial Targets: a versatile cell-free platform to characterize CAR T cell function <i>in vitro</i>
Xueting Wang, Nicholas J A Tokarew, Nadine Borgelt, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
November 19, 2025
Base edited skin equivalents with clinical potential for ex vivo correction of recessive dystrophic epidermolysis bullosa
Alex Bassons-Bascuñana, Blanca Duarte, Estela Méndez-Jiménez, et al.
Nature Communications
|
May 8, 2026
Simultaneous orthogonal cell engineering by a single CRISPR-Cas9 polyfunctional editor
Deborah Cipria, Tania Baccega, Miriana Rizzo, et al.
Nucleic Acids Research
|
April 29, 2025
Donor insertion into CX3CR1 allows epigenetic modulation of a constitutive promoter on hematopoietic stem cells and its activation upon myeloid differentiation
Iris Ramos-Hernández, Carla Fuster-García, Araceli Aguilar-González, et al.
Nature Methods
|
September 23, 2024
Effective genome editing with an enhanced ISDra2 TnpB system and deep learning-predicted ωRNAs
Kim Fabiano Marquart, Nicolas Mathis, Amina Mollaysa, et al.
Page
of 18