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Toni Cathomen

Showing results (161-170 of 172) with videos related to

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Frontiers in Immunology|June 13, 2024
Generating universal anti-CD19 CAR T cells with a defined memory phenotype by CRISPR/Cas9 editing and safety evaluation of the transcriptomeKristina Pavlovic, MDolores Carmona-Luque, Giulia I Corsi, et al.
Blood|March 17, 2024
Integration of ζ-deficient CARs into the CD3ζ gene conveys potent cytotoxicity in T and NK cellsJonas Kath, Clemens Franke, Vanessa Drosdek, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|June 26, 2021
Prediction and validation of hematopoietic stem and progenitor cell off-target editing in transplanted rhesus macaquesAisha A AlJanahi, Cicera R Lazzarotto, Shirley Chen, et al.
Cell Stem Cell|January 28, 2026
Lipid nanoparticle-based non-viral in situ gene editing of congenital ichthyosis-causing mutations in human skin modelsDilem Ceren Apaydin, Gaurav Sadhnani, Tiffany Carlaw, et al.
Molecular Therapy. Nucleic Acids|May 22, 2023
Editing the core region in HPFH deletions alters fetal and adult globin expression for treatment of β-hemoglobinopathiesVigneshwaran Venkatesan, Abisha Crystal Christopher, Manuel Rhiel, et al.
Molecular Cell|July 29, 2008
Rapid "open-source" engineering of customized zinc-finger nucleases for highly efficient gene modificationMorgan L Maeder, Stacey Thibodeau-Beganny, Anna Osiak, et al.
The Journal of Experimental Medicine|September 29, 2023
Epitope-engineered human hematopoietic stem cells are shielded from CD123-targeted immunotherapyRomina Marone, Emmanuelle Landmann, Anna Devaux, et al.
Human Gene Therapy|July 25, 2024
Improving the Assessment of Risk Factors Relevant to Potential Carcinogenicity of Gene Therapies: A Consensus ArticleJan C Klapwijk, Alberto Del Rio Espinola, Silvana Libertini, et al.
Nature Medicine|October 21, 2014
Autosomal dominant immune dysregulation syndrome in humans with CTLA4 mutationsDesirée Schubert, Claudia Bode, Rupert Kenefeck, et al.
Molecular Therapy. Nucleic Acids|November 30, 2023
Progress and harmonization of gene editing to treat human diseases: Proceeding of COST Action CA21113 GenE-HumDiAlessia Cavazza, Ayal Hendel, Rasmus O Bak, et al.
Pageof 18

Showing results (161-170 of 172) with videos related to

Sort By:
Pageof 18
Frontiers in Immunology|June 13, 2024
Generating universal anti-CD19 CAR T cells with a defined memory phenotype by CRISPR/Cas9 editing and safety evaluation of the transcriptomeKristina Pavlovic, MDolores Carmona-Luque, Giulia I Corsi, et al.
Blood|March 17, 2024
Integration of ζ-deficient CARs into the CD3ζ gene conveys potent cytotoxicity in T and NK cellsJonas Kath, Clemens Franke, Vanessa Drosdek, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|June 26, 2021
Prediction and validation of hematopoietic stem and progenitor cell off-target editing in transplanted rhesus macaquesAisha A AlJanahi, Cicera R Lazzarotto, Shirley Chen, et al.
Cell Stem Cell|January 28, 2026
Lipid nanoparticle-based non-viral in situ gene editing of congenital ichthyosis-causing mutations in human skin modelsDilem Ceren Apaydin, Gaurav Sadhnani, Tiffany Carlaw, et al.
Molecular Therapy. Nucleic Acids|May 22, 2023
Editing the core region in HPFH deletions alters fetal and adult globin expression for treatment of β-hemoglobinopathiesVigneshwaran Venkatesan, Abisha Crystal Christopher, Manuel Rhiel, et al.
Molecular Cell|July 29, 2008
Rapid "open-source" engineering of customized zinc-finger nucleases for highly efficient gene modificationMorgan L Maeder, Stacey Thibodeau-Beganny, Anna Osiak, et al.
The Journal of Experimental Medicine|September 29, 2023
Epitope-engineered human hematopoietic stem cells are shielded from CD123-targeted immunotherapyRomina Marone, Emmanuelle Landmann, Anna Devaux, et al.
Human Gene Therapy|July 25, 2024
Improving the Assessment of Risk Factors Relevant to Potential Carcinogenicity of Gene Therapies: A Consensus ArticleJan C Klapwijk, Alberto Del Rio Espinola, Silvana Libertini, et al.
Nature Medicine|October 21, 2014
Autosomal dominant immune dysregulation syndrome in humans with CTLA4 mutationsDesirée Schubert, Claudia Bode, Rupert Kenefeck, et al.
Molecular Therapy. Nucleic Acids|November 30, 2023
Progress and harmonization of gene editing to treat human diseases: Proceeding of COST Action CA21113 GenE-HumDiAlessia Cavazza, Ayal Hendel, Rasmus O Bak, et al.
Pageof 18