Showing results (51-60 of 65) with videos related to

Sort By:
Pageof 7
Molecular Therapy. Nucleic Acids|July 2, 2024
Targeted knock-in of NCF1 cDNA into the NCF2 locus leads to myeloid phenotypic correction of p47 -deficient chronic granulomatous diseaseKah Mun Siow, Merve Güngör, Dominik Wrona, et al.
Communications Biology|October 9, 2024
Gene editing of NCF1 loci is associated with homologous recombination and chromosomal rearrangementsFederica Raimondi, Kah Mun Siow, Dominik Wrona, et al.
Nature|September 22, 2006
Gene therapy: X-SCID transgene leukaemogenicityAdrian J Thrasher, H Bobby Gaspar, Christopher Baum, et al.
Blood|February 17, 2005
Leukemias following retroviral transfer of multidrug resistance 1 (MDR1) are driven by combinatorial insertional mutagenesisUte Modlich, Olga S Kustikova, Manfred Schmidt, et al.
Stem Cell Research|November 10, 2024
Eight induced pluripotent stem cell lines (iPSCs) derived from two patients with Leukocyte adhesion deficiency Type I (LAD I) with mutations in the ITGB2 geneJulia Fekadu-Siebald, Nina V Fuchs, Stella Zahn, et al.
Molecular Therapy. Nucleic Acids|July 7, 2023
Lentiviral gene therapy reverts GPIX expression and phenotype in Bernard-Soulier syndrome type CGonzalo Martinez-Navajas, Jorge Ceron-Hernandez, Iris Simon, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|February 15, 2007
Importance of murine study design for testing toxicity of retroviral vectors in support of phase I trialsElke Will, Jeff Bailey, Todd Schuesler, et al.
Cell Reports|October 5, 2022
Influenza A virus infection instructs hematopoiesis to megakaryocyte-lineage outputMarcel G E Rommel, Lisa Walz, Foteini Fotopoulou, et al.
Human Gene Therapy Methods|March 21, 2012
Identity, potency, in vivo viability, and scaling up production of lentiviral vector-induced dendritic cells for melanoma immunotherapyMudita Pincha, Bala Sai Sundarasetty, Gustavo Salguero, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|June 26, 2021
Predicting genotoxicity of viral vectors for stem cell gene therapy using gene expression-based machine learningAdrian Schwarzer, Steven R Talbot, Anton Selich, et al.
Pageof 7