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Clinical Genetics
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April 9, 2022
SHP2's gain-of-function in Werner syndrome causes childhood disease onset likely resulting from negative genetic interaction
Manuela Priolo, Valentina Palermo, Francesca Aiello, et al.
European Journal of Human Genetics : EJHG
|
January 8, 2026
Newly identified ARF3 variants strengthen the causal link between Golgi fragmentation and brain malformations
Valentina Muto, Giulia Fasano, Francesca Clementina Radio, et al.
Nature Genetics
|
July 15, 2014
Mutations in ZBTB20 cause Primrose syndrome
Viviana Cordeddu, Bert Redeker, Emilia Stellacci, et al.
American Journal of Medical Genetics. Part A
|
June 18, 2016
CREBBP mutations in individuals without Rubinstein-Taybi syndrome phenotype
Leonie A Menke, Martine J van Belzen, Marielle Alders, et al.
Brain : a Journal of Neurology
|
June 26, 2026
GIT1 loss of function causes a recognizable syndromic neurodevelopmental disorder
Pinella Failla, Valentina Muto, Antonella Lauri, et al.
Neurology
|
July 1, 2018
Biallelic <i>SQSTM1</i> mutations in early-onset, variably progressive neurodegeneration
Valentina Muto, Elisabetta Flex, Zachary Kupchinsky, et al.
Nature Communications
|
November 11, 2022
Dominant ARF3 variants disrupt Golgi integrity and cause a neurodevelopmental disorder recapitulated in zebrafish
Giulia Fasano, Valentina Muto, Francesca Clementina Radio, et al.
American Journal of Human Genetics
|
December 14, 2020
SCUBE3 loss-of-function causes a recognizable recessive developmental disorder due to defective bone morphogenetic protein signaling
Yuh-Charn Lin, Marcello Niceta, Valentina Muto, et al.
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Search research articles
Search
Showing results (11-20 of 18) with videos related to
Sort By:
Page
of 2
You have reached the last page of results.
This site can display upto 18 results.
Clinical Genetics
|
April 9, 2022
SHP2's gain-of-function in Werner syndrome causes childhood disease onset likely resulting from negative genetic interaction
Manuela Priolo, Valentina Palermo, Francesca Aiello, et al.
European Journal of Human Genetics : EJHG
|
January 8, 2026
Newly identified ARF3 variants strengthen the causal link between Golgi fragmentation and brain malformations
Valentina Muto, Giulia Fasano, Francesca Clementina Radio, et al.
Nature Genetics
|
July 15, 2014
Mutations in ZBTB20 cause Primrose syndrome
Viviana Cordeddu, Bert Redeker, Emilia Stellacci, et al.
American Journal of Medical Genetics. Part A
|
June 18, 2016
CREBBP mutations in individuals without Rubinstein-Taybi syndrome phenotype
Leonie A Menke, Martine J van Belzen, Marielle Alders, et al.
Brain : a Journal of Neurology
|
June 26, 2026
GIT1 loss of function causes a recognizable syndromic neurodevelopmental disorder
Pinella Failla, Valentina Muto, Antonella Lauri, et al.
Neurology
|
July 1, 2018
Biallelic <i>SQSTM1</i> mutations in early-onset, variably progressive neurodegeneration
Valentina Muto, Elisabetta Flex, Zachary Kupchinsky, et al.
Nature Communications
|
November 11, 2022
Dominant ARF3 variants disrupt Golgi integrity and cause a neurodevelopmental disorder recapitulated in zebrafish
Giulia Fasano, Valentina Muto, Francesca Clementina Radio, et al.
American Journal of Human Genetics
|
December 14, 2020
SCUBE3 loss-of-function causes a recognizable recessive developmental disorder due to defective bone morphogenetic protein signaling
Yuh-Charn Lin, Marcello Niceta, Valentina Muto, et al.
Page
of 2