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Human Gene Therapy|September 12, 2018
Gene Therapy for HemoglobinopathiesMarina Cavazzana, Fulvio Mavilio
Stem Cells and Development|May 5, 2026
Hematopoietic Stem Cell-Based Cell and Gene Therapy Beyond Monogenic DiseasesMasayuki Kai, Fulvio Mavilio
Molecular Therapy. Methods & Clinical Development|May 1, 2018
Preclinical Development of a Lentiviral Vector for Gene Therapy of X-Linked Severe Combined ImmunodeficiencyValentina Poletti, Sabine Charrier, Guillaume Corre, et al.
Hematology/Oncology Clinics of North America|September 13, 2017
Gene Therapy Approaches to HemoglobinopathiesGiuliana Ferrari, Marina Cavazzana, Fulvio Mavilio
Human Gene Therapy|January 22, 2013
Mechanisms of retroviral integration and mutagenesisAlessia Cavazza, Arianna Moiani, Fulvio Mavilio
Molecular Therapy. Methods & Clinical Development|December 12, 2018
Pre-clinical Development of a Lentiviral Vector Expressing the Anti-sickling βAS3 Globin for Gene Therapy for Sickle Cell DiseaseValentina Poletti, Fabrizia Urbinati, Sabine Charrier, et al.
Human Gene Therapy|September 11, 2018
Gene Therapy for Sickle Cell Disease: A Lentiviral Vector Comparison StudyFabrizia Urbinati, Beatriz Campo Fernandez, Katelyn E Masiuk, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|September 25, 2008
Correction of laminin-5 deficiency in human epidermal stem cells by transcriptionally targeted lentiviral vectorsFrancesca Di Nunzio, Giulietta Maruggi, Stefano Ferrari, et al.
Molecular Therapy. Nucleic Acids|April 24, 2023
Novel lentiviral vectors for gene therapy of sickle cell disease combining gene addition and gene silencing strategiesMégane Brusson, Anne Chalumeau, Pierre Martinucci, et al.
Plos One|May 16, 2015
Genome-Wide Definition of Promoter and Enhancer Usage during Neural Induction of Human Embryonic Stem CellsValentina Poletti, Alessia Delli Carri, Guidantonio Malagoli Tagliazucchi, et al.
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