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Cells|June 24, 2022
CFTR Rescue by Lumacaftor (VX-809) Induces an Extensive Reorganization of Mitochondria in the Cystic Fibrosis Bronchial EpitheliumClarissa Braccia, Josie A Christopher, Oliver M Crook, et al.Journal of Cystic Fibrosis : Official Journal of the European Cystic Fibrosis Society|May 24, 2024
Tezacaftor is a direct inhibitor of sphingolipid delta-4 desaturase enzyme (DEGS)Dinu Zinovie Ciobanu, Nara Liessi, Valeria Tomati, et al.Journal of Medicinal Chemistry|October 22, 2015
Hit Optimization of 5-Substituted-N-(piperidin-4-ylmethyl)-1H-indazole-3-carboxamides: Potent Glycogen Synthase Kinase-3 (GSK-3) Inhibitors with in Vivo Activity in Model of Mood DisordersGuido Furlotti, Maria Alessandra Alisi, Nicola Cazzolla, et al.American Journal of Respiratory Cell and Molecular Biology|September 23, 2024
Distinct Responses of Cystic Fibrosis Epithelial Cells to SARS-CoV-2 and Influenza A VirusIsabel Pagani, Arianna Venturini, Valeria Capurro, et al.Journal of Cystic Fibrosis : Official Journal of the European Cystic Fibrosis Society|November 16, 2025
Correcting CFTR mRNA splicing defects with the plant cytokine kinetin and its analoguesValeria Rimoldi, Giulia Soldà, Anita Capalbo, et al.International Journal of Molecular Sciences|June 2, 2021
Partial Rescue of F508del-CFTR Stability and Trafficking Defects by Double Corrector TreatmentValeria Capurro, Valeria Tomati, Elvira Sondo, et al.International Journal of Molecular Sciences|March 25, 2022
The L467F-F508del Complex Allele Hampers Pharmacological Rescue of Mutant CFTR by Elexacaftor/Tezacaftor/Ivacaftor in Cystic Fibrosis Patients: The Value of the Ex Vivo Nasal Epithelial Model to Address Non-Responders to CFTR-Modulating DrugsElvira Sondo, Federico Cresta, Cristina Pastorino, et al.ACS Chemical Biology|April 16, 2015
A Potent Systemically Active N-Acylethanolamine Acid Amidase Inhibitor that Suppresses Inflammation and Human Macrophage ActivationAlison Ribeiro, Silvia Pontis, Luisa Mengatto, et al.Journal of Cystic Fibrosis : Official Journal of the European Cystic Fibrosis Society|December 21, 2022
Rescue by elexacaftor-tezacaftor-ivacaftor of the G1244E cystic fibrosis mutation's stability and gating defects are dependent on cell backgroundValeria Tomati, Stefano Costa, Valeria Capurro, et al.ERJ Open Research|May 28, 2025
Deleterious effect of <i>Pseudomonas aeruginosa</i> on F508del-CFTR rescued by elexacaftor/tezacaftor/ivacaftor is clinical strain-dependent in patient-derived nasal cellsCaterina Allegretta, Enza Montemitro, Maria Noemi Sgobba, et al.Pageof 5