Showing results (21-30 of 26) with videos related to
Sort By:
Pageof 3
You have reached the last page of results.This site can display upto 26 results.
Drug Discovery Today|October 9, 2017
Nonclinical data supporting orphan medicinal product designations: lessons from rare neurological conditionsMaria E Sheean, Violeta Stoyanova-Beninska, Giuseppe Capovilla, et al.Drug Discovery Today|April 29, 2020
Assessment of significant benefit for orphan medicinal products by European regulators may support subsequent relative effectiveness assessments by health technology assessment organizationsRick A Vreman, Angela S de Ruijter, Anna Zawada, et al.Drug Discovery Today|November 10, 2019
Nonclinical data supporting orphan medicinal product designations in the area of rare infectious diseasesMaria E Sheean, Eva Malikova, Dinah Duarte, et al.Cancer Management and Research|March 6, 2025
Drug Repurposing in Pancreatic Cancer: A Multi-Stakeholder Perspective to Improve Treatment Options for Pancreatic Cancer PatientsEvelyn Hewitt, Gauthier Bouche, Alexandre Costa Alencar, et al.Clinical Pharmacology and Therapeutics|July 4, 2024
Real-World Evidence to Support EU Regulatory Decision Making-Results From a Pilot of Regulatory Use CasesStefanie Prilla, Sophie Groeneveld, Alexandra Pacurariu, et al.The Lancet. Neurology|June 16, 2016
Stakeholder cooperation to overcome challenges in orphan medicine development: the example of Duchenne muscular dystrophyVolker Straub, Pavel Balabanov, Kate Bushby, et al.Pageof 3