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Skeletal Muscle
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December 4, 2015
Elusive sources of variability of dystrophin rescue by exon skipping
Maria Candida Vila, Margaret Benny Klimek, James S Novak, et al.
Plos One
|
March 4, 2014
Quantitative magnetic resonance imaging in limb-girdle muscular dystrophy 2I: a multinational cross-sectional study
Tracey A Willis, Kieren G Hollingsworth, Anna Coombs, et al.
Cell Death & Disease
|
September 6, 2023
Decoding the transcriptome of Duchenne muscular dystrophy to the single nuclei level reveals clinical-genetic correlations
Xavier Suárez-Calvet, Esther Fernández-Simón, Daniel Natera, et al.
Journal of Neurology
|
September 27, 2019
European muscle MRI study in limb girdle muscular dystrophy type R1/2A (LGMDR1/LGMD2A)
Andrea Barp, Pascal Laforet, Luca Bello, et al.
European Journal of Human Genetics : EJHG
|
June 4, 2025
Novel HSPB8 mutations in severe early-onset myopathy with involvement of respiratory and cardiac muscles cause proteostasis defects in cell models
Barbara Tedesco, Stojan Peric, Goknur Selen Kocak, et al.
Journal of Cachexia, Sarcopenia and Muscle
|
August 15, 2025
High-Density Lipoprotein-Associated Cholesterol Abnormalities in a Clinical Outcomes Study of Dysferlin-Deficient Limb-Girdle Muscular Dystrophy Type R2
Zoe White, Laura Rufibach, Heather Gordish Dressman, et al.
Brain : a Journal of Neurology
|
November 7, 2016
Recessive mutations in the kinase ZAK cause a congenital myopathy with fibre type disproportion
Nasim Vasli, Elizabeth Harris, Jason Karamchandani, et al.
Neuromuscular Disorders : NMD
|
February 17, 2019
Safety, tolerability, pharmacokinetics, pharmacodynamics, and exploratory efficacy of the novel enzyme replacement therapy avalglucosidase alfa (neoGAA) in treatment-naïve and alglucosidase alfa-treated patients with late-onset Pompe disease: A phase 1, open-label, multicenter, multinational, ascending dose study
Loren D M Pena, Richard J Barohn, Barry J Byrne, et al.
Neuromuscular Disorders : NMD
|
August 23, 2024
Performance of upper limb entry item to predict forced vital capacity in dysferlin-deficient limb girdle muscular dystrophy
Holly Borland, Ursula Moore, Heather Gordish Dressman, et al.
Neurology. Genetics
|
July 13, 2023
Longitudinal Analysis of Respiratory Function of Different Types of Limb Girdle Muscular Dystrophies Reveals Independent Trajectories
Robert Muni-Lofra, Eduard Juanola-Mayos, Marianela Schiava, et al.
Page
of 38
Search research articles
Search
Showing results (251-260 of 374) with videos related to
Sort By:
Page
of 38
Skeletal Muscle
|
December 4, 2015
Elusive sources of variability of dystrophin rescue by exon skipping
Maria Candida Vila, Margaret Benny Klimek, James S Novak, et al.
Plos One
|
March 4, 2014
Quantitative magnetic resonance imaging in limb-girdle muscular dystrophy 2I: a multinational cross-sectional study
Tracey A Willis, Kieren G Hollingsworth, Anna Coombs, et al.
Cell Death & Disease
|
September 6, 2023
Decoding the transcriptome of Duchenne muscular dystrophy to the single nuclei level reveals clinical-genetic correlations
Xavier Suárez-Calvet, Esther Fernández-Simón, Daniel Natera, et al.
Journal of Neurology
|
September 27, 2019
European muscle MRI study in limb girdle muscular dystrophy type R1/2A (LGMDR1/LGMD2A)
Andrea Barp, Pascal Laforet, Luca Bello, et al.
European Journal of Human Genetics : EJHG
|
June 4, 2025
Novel HSPB8 mutations in severe early-onset myopathy with involvement of respiratory and cardiac muscles cause proteostasis defects in cell models
Barbara Tedesco, Stojan Peric, Goknur Selen Kocak, et al.
Journal of Cachexia, Sarcopenia and Muscle
|
August 15, 2025
High-Density Lipoprotein-Associated Cholesterol Abnormalities in a Clinical Outcomes Study of Dysferlin-Deficient Limb-Girdle Muscular Dystrophy Type R2
Zoe White, Laura Rufibach, Heather Gordish Dressman, et al.
Brain : a Journal of Neurology
|
November 7, 2016
Recessive mutations in the kinase ZAK cause a congenital myopathy with fibre type disproportion
Nasim Vasli, Elizabeth Harris, Jason Karamchandani, et al.
Neuromuscular Disorders : NMD
|
February 17, 2019
Safety, tolerability, pharmacokinetics, pharmacodynamics, and exploratory efficacy of the novel enzyme replacement therapy avalglucosidase alfa (neoGAA) in treatment-naïve and alglucosidase alfa-treated patients with late-onset Pompe disease: A phase 1, open-label, multicenter, multinational, ascending dose study
Loren D M Pena, Richard J Barohn, Barry J Byrne, et al.
Neuromuscular Disorders : NMD
|
August 23, 2024
Performance of upper limb entry item to predict forced vital capacity in dysferlin-deficient limb girdle muscular dystrophy
Holly Borland, Ursula Moore, Heather Gordish Dressman, et al.
Neurology. Genetics
|
July 13, 2023
Longitudinal Analysis of Respiratory Function of Different Types of Limb Girdle Muscular Dystrophies Reveals Independent Trajectories
Robert Muni-Lofra, Eduard Juanola-Mayos, Marianela Schiava, et al.
Page
of 38