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Pediatric Neurology|September 22, 2014
Experimental therapies in the murine model of globoid cell leukodystrophyYedda Li, Mark S Sands
Nature Genetics|March 10, 2009
The impact of copy number variation on local gene expression in mouse hematopoietic stem and progenitor cellsPatrick Cahan, Yedda Li, Masayo Izumi, et al.
Neurotherapeutics : the Journal of the American Society for Experimental Neurotherapeutics|September 14, 2024
Gene therapy for the leukodystrophies: From preclinical animal studies to clinical trialsJasna Metovic, Yedda Li, Yi Gong, et al.
Molecular Therapy. Methods & Clinical Development|August 1, 2015
Generation of a stable packaging cell line producing high-titer PPT-deleted integration-deficient lentiviral vectorsPeirong Hu, Yedda Li, Mark S Sands, et al.
Neurology|February 7, 2025
Disease Burden in Female Patients With X-Linked AdrenoleukodystrophyNatalie R Grant, Yedda Li, Lizbeth De La Rosa Abreu, et al.
Annals of Neurology|December 8, 2023
Role of Basal Forebrain Neurons in Adrenomyeloneuropathy in Mice and HumansYi Gong, Fiza Laheji, Anna Berenson, et al.
Journal of Neuroscience Research|September 18, 2016
Hematopoietic Stem cell transplantation and lentiviral vector-based gene therapy for Krabbe's disease: Present convictions and future prospectsPeirong Hu, Yedda Li, Nana Nikolaishvili-Feinberg, et al.
The Journal of Neuroscience : the Official Journal of the Society for Neuroscience|April 24, 2015
Mechanism-based combination treatment dramatically increases therapeutic efficacy in murine globoid cell leukodystrophyJacqueline A Hawkins-Salsbury, Lauren Shea, Xuntian Jiang, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|January 3, 2021
Enhanced Efficacy and Increased Long-Term Toxicity of CNS-Directed, AAV-Based Combination Therapy for Krabbe DiseaseYedda Li, Christopher A Miller, Lauren K Shea, et al.
Proceedings of the National Academy of Sciences of the United States of America|September 19, 2019
Genetic ablation of acid ceramidase in Krabbe disease confirms the psychosine hypothesis and identifies a new therapeutic targetYedda Li, Yue Xu, Bruno A Benitez, et al.
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