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Acta Biochimica Et Biophysica Sinica|January 6, 2025
MYB represses ζ-globin expression through upregulating ETO2Zejun Dong, Yuhua Ye, Wei Zhang, et al.
Experimental Hematology & Oncology|March 29, 2025
A one-base therapeutic insertion in the HBG2 distal promoter reactivates γ-globin expressionXiuqin Bao, Yuanyi Gao, Xiaoyi Chen, et al.
Molecular Therapy. Nucleic Acids|December 6, 2024
Efficient and in situ correction of hemoglobin Constant Spring mutation by prime editing in human hematopoietic cellsCongwen Shao, Qing Liu, Jinchao Xu, et al.
Annals of Hematology|February 27, 2025
Rapid detection of genetic modifiers of β-thalassemia based on MALDI-TOF MSLi Huang, Qianqian Zhang, Yuhua Ye, et al.
Journal of Genetics and Genomics = Yi Chuan Xue Bao|November 9, 2024
Activation of γ-globin expression by a common variant disrupting IKAROS-binding motif in β-thalassemiaHualei Luo, Jueheng Wang, Lang Qin, et al.
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