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Brain : a Journal of Neurology|June 17, 2008
Mutation of FIG4 causes a rapidly progressive, asymmetric neuronal degenerationXuebao Zhang, Clement Y Chow, Zarife Sahenk, et al.Journal of Neuromuscular Diseases|November 19, 2016
Follistatin Gene Therapy Improves Ambulation in Becker Muscular DystrophySamiah A Al-Zaidy, Zarife Sahenk, Louise R Rodino-Klapac, et al.Neurodegenerative Disease Management|September 2, 2021
Unmet needs and evolving treatment for limb girdle muscular dystrophiesEric Pozsgai, Danielle Griffin, Rachael Potter, et al.Molecular Therapy. Advances|May 15, 2026
Autophagy activation via BAG3 gene therapy improves phenotype in a mouse model of LGMD1ABurcak Ozes, Lingying Tong, Kyle Moss, et al.Brain and Behavior|September 22, 2018
Efficacy of exogenous pyruvate in Trembler<sup>J</sup> mouse model of Charcot-Marie-Tooth neuropathyZarife Sahenk, Mehmet E Yalvac, Jakkrit Amornvit, et al.Human Molecular Genetics|August 14, 2010
A humanized Smn gene containing the SMN2 nucleotide alteration in exon 7 mimics SMN2 splicing and the SMA disease phenotypeJordan T Gladman, Thomas W Bebee, Chris Edwards, et al.Gene Therapy|February 19, 2025
AAV1.NT3 gene therapy mitigates the severity of autoimmune encephalomyelitis in the mouse model for multiple sclerosisLingying Tong, Burcak Ozes, Kyle Moss, et al.Journal of Neuropathology and Experimental Neurology|April 16, 2026
The NORAD-Pumilio regulatory axis in the evolution of inclusion body myositisLingying Tong, Burcak Ozes, Kyle Moss, et al.Neuroscience Letters|May 22, 2012
Gene therapy for muscular dystrophy: lessons learned and path forwardJerry R Mendell, Louise Rodino-Klapac, Zarife Sahenk, et al.Molecular Therapy. Methods & Clinical Development|September 13, 2021
Systemic delivery of AAVrh74.tMCK.hCAPN3 rescues the phenotype in a mouse model for LGMD2A/R1Zarife Sahenk, Burcak Ozes, Darren Murrey, et al.Pageof 8