Showing results (1971-1980 of 4,138) with videos related to

Sort By:
Pageof 414
Human Gene Therapy|January 10, 2025
Novel Cystic Fibrosis Ferret Model Enables Visualization of CFTR Expression Cells and Genetic CFTR ReactivationFeng Yuan, Xingshen Sun, Soo Yeun Park, et al.
Human Gene Therapy|August 28, 2024
Adeno-Associated Virus Vectors-a Target of Cellular and Humoral Immunity-are Expanding Their Reach Toward Hematopoietic Stem Cell Modification and ImmunotherapiesAngela E Araujo, Martin Bentler, Xabier Perez Garmendia, et al.
Human Gene Therapy|August 19, 2024
Inhalation of SP-101 Followed by Inhaled Doxorubicin Results in Robust and Durable hCFTRΔR Transgene Expression in the Airways of Wild-Type and Cystic Fibrosis FerretsKatherine J D A Excoffon, Mark D Smith, Lillian Falese, et al.
Human Gene Therapy|August 19, 2024
SP-101, A Novel Adeno-Associated Virus Gene Therapy for the Treatment of Cystic Fibrosis, Mediates Functional Correction of Primary Human Airway Epithelia From Donors with Cystic FibrosisKatherine J D A Excoffon, Shen Lin, Poornima Kotha Lakshmi Narayan, et al.
Human Gene Therapy|August 16, 2024
Alpharetroviral Vector-Mediated Gene Therapy for IL7RA-Deficient Severe Combined ImmunodeficiencyTeng-Cheong Ha, Michael A Morgan, Adrian J Thrasher, et al.
Human Gene Therapy|August 14, 2024
Lipid Nanoparticles for Nucleic Acid Delivery Beyond the LiverNadine Saber, Mariona Estapé Senti, Raymond M Schiffelers
Human Gene Therapy|June 15, 2024
Peripheral Cellular Immune Responses Induced by Subretinal Adeno-Associated Virus Gene Transfer Can Be Restrained by the Subretinal-Associated Immune Inhibition MechanismJulie Vendomèle, Gaëlle Anne Chauveau, Deniz Dalkara, et al.
Human Gene Therapy|August 25, 2023
Biotechnological Advances in Gene Therapy of Hematopoietic Stem Cells: Systematic Review and Meta-AnalysisCarla Cristina Pedrosa de Lira de Morais, Daniela Prado Cunha, Zilton Farias Meira de Vasconcelos
Human Gene Therapy|August 25, 2023
Adeno-Associated Viral Vector-Delivered Pannexin-1 Mimetic Peptide Alleviates Airway Inflammation in an Allergen-Sensitized Mouse ModelYung-An Huang, Jeng-Chang Chen, Pei-Chuan Chiang, et al.
Human Gene Therapy|August 29, 2023
Clustered Regularly Interspaced Short Palindromic Repeats and Clustered Regularly Interspaced Short Palindromic Repeats-Associated Protein 9 System: Factors Affecting Precision Gene Editing Efficiency and Optimization StrategiesJiawen Li, Chuxi Tang, Guozheng Liang, et al.
Pageof 414