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Human Gene Therapy|April 25, 2019
Safe and Sustained Expression of Human Iduronidase After Intrathecal Administration of Adeno-Associated Virus Serotype 9 in Infant Rhesus MonkeysJuliette Hordeaux, Christian Hinderer, Elizabeth L Buza, et al.Human Gene Therapy|July 20, 2018
Purification of mRNA Encoding Chimeric Antigen Receptor Is Critical for Generation of a Robust T-Cell ResponseJessica B Foster, Namrata Choudhari, Jessica Perazzelli, et al.Human Gene Therapy|July 21, 2018
Using DNA Immunization to Elicit Monoclonal Antibodies in Mice, Rabbits, and HumansShuying Liu, Shixia Wang, Shan LuHuman Gene Therapy|August 3, 2018
AAV-Mediated TAZ Gene Replacement Restores Mitochondrial and Cardioskeletal Function in Barth SyndromeSilveli Suzuki-Hatano, Madhurima Saha, Skylar A Rizzo, et al.Human Gene Therapy|April 28, 2017
Effect of Intravesical Liposome-Based Nerve Growth Factor Antisense Therapy on Bladder Overactivity and Nociception in a Rat Model of Cystitis Induced by Hydrogen PeroxideTsuyoshi Majima, Pradeep Tyagi, Koji Dogishi, et al.Human Gene Therapy|May 10, 2018
Heparan Sulfate Binding Coxsackievirus B3 Strain PD: A Novel Avirulent Oncolytic Agent Against Human Colorectal CarcinomaAhmet Hazini, Markian Pryshliak, Vanessa Brückner, et al.Human Gene Therapy|May 24, 2018
Effect of Human Wnt10b Transgene Overexpression on Peri-Implant Osteogenesis in Ovariectomized RatsHanghang Liu, Nian Zhang, Yao Liu, et al.Human Gene Therapy|March 10, 2010
Transduction of human antigen-presenting cells with integrase-defective lentiviral vector enables functional expansion of primed antigen-specific CD8(+) T cellsDonatella R M Negri, Roberta Bona, Zuleika Michelini, et al.Human Gene Therapy|March 13, 2010
An all-feline retroviral packaging system for transduction of human cellsRaymond T Doty, Kathleen M Sabo, Jing Chen, et al.Human Gene Therapy|April 13, 2018
CRISPR/Cas9 Inhibits Multiple Steps of HIV-1 InfectionLijuan Yin, Siqi Hu, Shan Mei, et al.Pageof 413