Human gene therapy - JoVE Visualize

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Human Gene Therapy|April 12, 2011

Optimizing promoters for recombinant adeno-associated virus-mediated gene expression in the peripheral and central nervous system using self-complementary vectorsSteven J Gray, Stacey B Foti, Joel W Schwartz, et al.

Human Gene Therapy|August 5, 2026

Suppression of AAV-Delivered Transgene Expression Using Artificial MicroRNAs Delivered by an Alternative AAV SerotypeMiguel de Mulder Rougvie, Mara R Kebret, Youjun Wu, et al.

Human Gene Therapy|July 16, 2026

Dichotomies in Ex Vivo and In Vivo Performance of Receptor-Binding Mutants of Adeno-Associated Virus VectorsOlaniyi Olarewaju, Martin Bentler, Jacqueline Breuer, et al.

Human Gene Therapy|August 5, 2026

Safety, Tolerability, and Efficacy of a Prophylactic Sirolimus Protocol for Patients Receiving Delandistrogene Moxeparvovec-Rokl Gene TherapyZahraa Siddiqui, Serena Neumann, Daniel Guillen, et al.

Human Gene Therapy|August 3, 2026

Novel VSV-G Variants with Enhanced Blinding for Targeted Delivery of Lentiviral VectorsFelix L Warnecke, Moritz Ertelt, Anjali Shrivastava, et al.

Human Gene Therapy|August 17, 2026

Durational Study of Persistent Transduction of Rhesus Macaque Lung and Other Organs Following Single Dosing with AAV1-CFTRPrajita Paul, Tanvi Sharma, Masoud Afshani, et al.

Human Gene Therapy|August 24, 2026

Engineering Human Hematopoietic Stem and Progenitor Cells for Antigen Expression in Antigen-Presenting CellsClara Heider, Meg Louise Donovan, Carina Walpole, et al.

Human Gene Therapy|September 16, 2026

Development of an AAV-Encoded Adenine Base Editor for Duchenne Muscular DystrophyIna Luksch, Christine M Poch, Aylin Mayer, et al.

Human Gene Therapy|July 19, 2003

Construction of a cytomegalovirus-based amplicon: a vector with a unique transfer capacityEva Maria Borst, Martin Messerle

Human Gene Therapy|July 19, 2003

Genetic correction of DNA repair-deficient/cancer-prone xeroderma pigmentosum group C keratinocytesCatherine Arnaudeau-Bégard, Florence Brellier, Odile Chevallier-Lagente, et al.

Pageof 413

Showing results (3041-3050 of 4,130) with videos related to

Sort By:

Pageof 413

Human Gene Therapy|April 12, 2011

Optimizing promoters for recombinant adeno-associated virus-mediated gene expression in the peripheral and central nervous system using self-complementary vectorsSteven J Gray, Stacey B Foti, Joel W Schwartz, et al.

Human Gene Therapy|August 5, 2026

Suppression of AAV-Delivered Transgene Expression Using Artificial MicroRNAs Delivered by an Alternative AAV SerotypeMiguel de Mulder Rougvie, Mara R Kebret, Youjun Wu, et al.

Human Gene Therapy|July 16, 2026

Dichotomies in Ex Vivo and In Vivo Performance of Receptor-Binding Mutants of Adeno-Associated Virus VectorsOlaniyi Olarewaju, Martin Bentler, Jacqueline Breuer, et al.

Human Gene Therapy|August 5, 2026

Safety, Tolerability, and Efficacy of a Prophylactic Sirolimus Protocol for Patients Receiving Delandistrogene Moxeparvovec-Rokl Gene TherapyZahraa Siddiqui, Serena Neumann, Daniel Guillen, et al.

Human Gene Therapy|August 3, 2026

Novel VSV-G Variants with Enhanced Blinding for Targeted Delivery of Lentiviral VectorsFelix L Warnecke, Moritz Ertelt, Anjali Shrivastava, et al.

Human Gene Therapy|August 17, 2026

Durational Study of Persistent Transduction of Rhesus Macaque Lung and Other Organs Following Single Dosing with AAV1-CFTRPrajita Paul, Tanvi Sharma, Masoud Afshani, et al.

Human Gene Therapy|August 24, 2026

Engineering Human Hematopoietic Stem and Progenitor Cells for Antigen Expression in Antigen-Presenting CellsClara Heider, Meg Louise Donovan, Carina Walpole, et al.

Human Gene Therapy|September 16, 2026

Development of an AAV-Encoded Adenine Base Editor for Duchenne Muscular DystrophyIna Luksch, Christine M Poch, Aylin Mayer, et al.

Human Gene Therapy|July 19, 2003

Construction of a cytomegalovirus-based amplicon: a vector with a unique transfer capacityEva Maria Borst, Martin Messerle

Human Gene Therapy|July 19, 2003

Genetic correction of DNA repair-deficient/cancer-prone xeroderma pigmentosum group C keratinocytesCatherine Arnaudeau-Bégard, Florence Brellier, Odile Chevallier-Lagente, et al.

Pageof 413