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JIMD Reports
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November 20, 2019
A mutation in mannose-phosphate-dolichol utilization defect 1 reveals clinical symptoms of congenital disorders of glycosylation type I and dystroglycanopathy
Walinka van Tol, Angel Ashikov, Eckhard Korsch, et al.
JIMD Reports
|
March 11, 2020
Cystathionine beta synthase deficiency and brain edema associated with methionine excess under betaine supplementation: Four new cases and a review of the evidence
Bernd C Schwahn, Thomas Scheffner, Hedwig Stepman, et al.
JIMD Reports
|
December 3, 2019
A case of secondary acute myeloid leukemia on a background of glycogen storage disease with chronic neutropenia treated with granulocyte colony stimulating factor
Dina Khalaf, Heather Bell, David Dale, et al.
JIMD Reports
|
June 17, 2025
Exploratory Study on the Challenges of Newborn Screening for Lysosomal Storage Disorders Emphasizes the Need for Multitier Testing and Collaborative Approaches to Management
A Terrell, K Sapp, B Graham, et al.
JIMD Reports
|
July 8, 2025
Cardiac Transplantation Does Not Improve Exercise Tolerance, Muscle Mass, or Substrate Metabolism in Barth Syndrome
W Todd Cade, Kathryn L Bohnert, Linda R Peterson, et al.
JIMD Reports
|
December 30, 2025
A Multisystem Perspective of Pediatric Cell Trafficking Disorders: Within the Cells, Beneath the Signs
Merve Yoldaş Çelik, Burcu Köşeci, Ezgi Burgaç, et al.
JIMD Reports
|
December 29, 2025
Reversing Acute Cardiomyopathy With Coenzyme Q10 Supplementation in Cobalamin B Disease: A Case Report and Literature Review
Dalia Said, Aisha Al Shamsi
JIMD Reports
|
February 6, 2026
Mitochondrial Dysfunction in Propionic Acidemia: A Case-Report and Review of the Literature
Brandon K Walther, Brittany M Murray, Poornima Pandiyan, et al.
JIMD Reports
|
May 14, 2025
Atypical MEGDHEL Syndrome: A Milder Phenotype With Hepatic Presentation and Failure to Thrive Associated With a Homozygous Nonsense Variant of <i>SERAC1</i>
Rita Marchante Pita, Raquel Amaral, Laura Vilarinho, et al.
JIMD Reports
|
May 14, 2025
Successful Pregnancy Management of a Woman With Severe Methylmalonic Acidemia
M Woidy, K Tsiakas, M Mahmud, et al.
Page
of 125
Search research articles
Search
Showing results (1001-1010 of 1,250) with videos related to
Sort By:
Page
of 125
JIMD Reports
|
November 20, 2019
A mutation in mannose-phosphate-dolichol utilization defect 1 reveals clinical symptoms of congenital disorders of glycosylation type I and dystroglycanopathy
Walinka van Tol, Angel Ashikov, Eckhard Korsch, et al.
JIMD Reports
|
March 11, 2020
Cystathionine beta synthase deficiency and brain edema associated with methionine excess under betaine supplementation: Four new cases and a review of the evidence
Bernd C Schwahn, Thomas Scheffner, Hedwig Stepman, et al.
JIMD Reports
|
December 3, 2019
A case of secondary acute myeloid leukemia on a background of glycogen storage disease with chronic neutropenia treated with granulocyte colony stimulating factor
Dina Khalaf, Heather Bell, David Dale, et al.
JIMD Reports
|
June 17, 2025
Exploratory Study on the Challenges of Newborn Screening for Lysosomal Storage Disorders Emphasizes the Need for Multitier Testing and Collaborative Approaches to Management
A Terrell, K Sapp, B Graham, et al.
JIMD Reports
|
July 8, 2025
Cardiac Transplantation Does Not Improve Exercise Tolerance, Muscle Mass, or Substrate Metabolism in Barth Syndrome
W Todd Cade, Kathryn L Bohnert, Linda R Peterson, et al.
JIMD Reports
|
December 30, 2025
A Multisystem Perspective of Pediatric Cell Trafficking Disorders: Within the Cells, Beneath the Signs
Merve Yoldaş Çelik, Burcu Köşeci, Ezgi Burgaç, et al.
JIMD Reports
|
December 29, 2025
Reversing Acute Cardiomyopathy With Coenzyme Q10 Supplementation in Cobalamin B Disease: A Case Report and Literature Review
Dalia Said, Aisha Al Shamsi
JIMD Reports
|
February 6, 2026
Mitochondrial Dysfunction in Propionic Acidemia: A Case-Report and Review of the Literature
Brandon K Walther, Brittany M Murray, Poornima Pandiyan, et al.
JIMD Reports
|
May 14, 2025
Atypical MEGDHEL Syndrome: A Milder Phenotype With Hepatic Presentation and Failure to Thrive Associated With a Homozygous Nonsense Variant of <i>SERAC1</i>
Rita Marchante Pita, Raquel Amaral, Laura Vilarinho, et al.
JIMD Reports
|
May 14, 2025
Successful Pregnancy Management of a Woman With Severe Methylmalonic Acidemia
M Woidy, K Tsiakas, M Mahmud, et al.
Page
of 125