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JIMD Reports
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July 14, 2021
Cerebral folate deficiency in two siblings caused by biallelic variants including a novel mutation of <i>FOLR1</i> gene: Intrafamilial heterogeneity following early treatment and the role of ketogenic diet
Maria T Papadopoulou, Efterpi Dalpa, Michalis Portokalas, et al.
JIMD Reports
|
June 22, 2018
Stability of the ABCD1 Protein with a Missense Mutation: A Novel Approach to Finding Therapeutic Compounds for X-Linked Adrenoleukodystrophy
Masashi Morita, Shun Matsumoto, Airi Sato, et al.
JIMD Reports
|
May 1, 2017
Heterogeneous Phenotypes in Lipid Storage Myopathy Due to ETFDH Gene Mutations
Corrado Angelini, Daniela Tavian, Sara Missaglia
JIMD Reports
|
April 15, 2018
Serum Amino Acid Profiling in Citrin-Deficient Children Exhibiting Normal Liver Function During the Apparently Healthy Period
Teruo Miyazaki, Hironori Nagasaka, Haruki Komatsu, et al.
JIMD Reports
|
April 15, 2018
Reduced Muscle Strength in Barth Syndrome May Be Improved by Resistance Exercise Training: A Pilot Study
Adam J Bittel, Kathryn L Bohnert, Dominic N Reeds, et al.
JIMD Reports
|
July 8, 2017
Peripheral Neuropathy, Episodic Rhabdomyolysis, and Hypoparathyroidism in a Patient with Mitochondrial Trifunctional Protein Deficiency
Peter van Vliet, Annelies E Berden, Mojca K M van Schie, et al.
JIMD Reports
|
June 21, 2018
Extrapolation of Variant Phase in Mitochondrial Short-Chain Enoyl-CoA Hydratase (ECHS1) Deficiency
Colleen M Carlston, Sacha Ferdinandusse, Judith A Hobert, et al.
JIMD Reports
|
June 27, 2019
Genotype and phenotype classification of 29 patients affected by Krabbe disease
Anna M H Madsen, Flemming Wibrand, Allan M Lund, et al.
JIMD Reports
|
June 27, 2019
Validation of a therapeutic range for nitisinone in patients treated for tyrosinemia type 1 based on reduction of succinylacetone excretion
Rhona M Jack, C Ronald Scott
JIMD Reports
|
June 27, 2019
Formation of 3-hydroxyglutaric acid in glutaric aciduria type I: in vitro participation of medium chain acyl-CoA dehydrogenase
Verena Peters, Marina Morath, Matthias Mack, et al.
Page
of 127
Search research articles
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Showing results (101-110 of 1,270) with videos related to
Sort By:
Page
of 127
JIMD Reports
|
July 14, 2021
Cerebral folate deficiency in two siblings caused by biallelic variants including a novel mutation of <i>FOLR1</i> gene: Intrafamilial heterogeneity following early treatment and the role of ketogenic diet
Maria T Papadopoulou, Efterpi Dalpa, Michalis Portokalas, et al.
JIMD Reports
|
June 22, 2018
Stability of the ABCD1 Protein with a Missense Mutation: A Novel Approach to Finding Therapeutic Compounds for X-Linked Adrenoleukodystrophy
Masashi Morita, Shun Matsumoto, Airi Sato, et al.
JIMD Reports
|
May 1, 2017
Heterogeneous Phenotypes in Lipid Storage Myopathy Due to ETFDH Gene Mutations
Corrado Angelini, Daniela Tavian, Sara Missaglia
JIMD Reports
|
April 15, 2018
Serum Amino Acid Profiling in Citrin-Deficient Children Exhibiting Normal Liver Function During the Apparently Healthy Period
Teruo Miyazaki, Hironori Nagasaka, Haruki Komatsu, et al.
JIMD Reports
|
April 15, 2018
Reduced Muscle Strength in Barth Syndrome May Be Improved by Resistance Exercise Training: A Pilot Study
Adam J Bittel, Kathryn L Bohnert, Dominic N Reeds, et al.
JIMD Reports
|
July 8, 2017
Peripheral Neuropathy, Episodic Rhabdomyolysis, and Hypoparathyroidism in a Patient with Mitochondrial Trifunctional Protein Deficiency
Peter van Vliet, Annelies E Berden, Mojca K M van Schie, et al.
JIMD Reports
|
June 21, 2018
Extrapolation of Variant Phase in Mitochondrial Short-Chain Enoyl-CoA Hydratase (ECHS1) Deficiency
Colleen M Carlston, Sacha Ferdinandusse, Judith A Hobert, et al.
JIMD Reports
|
June 27, 2019
Genotype and phenotype classification of 29 patients affected by Krabbe disease
Anna M H Madsen, Flemming Wibrand, Allan M Lund, et al.
JIMD Reports
|
June 27, 2019
Validation of a therapeutic range for nitisinone in patients treated for tyrosinemia type 1 based on reduction of succinylacetone excretion
Rhona M Jack, C Ronald Scott
JIMD Reports
|
June 27, 2019
Formation of 3-hydroxyglutaric acid in glutaric aciduria type I: in vitro participation of medium chain acyl-CoA dehydrogenase
Verena Peters, Marina Morath, Matthias Mack, et al.
Page
of 127