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JIMD Reports
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November 17, 2017
Three Cases of Hereditary Tyrosinaemia Type 1: Neuropsychiatric Outcomes and Brain Imaging Following Treatment with NTBC
Helen Walker, Mervi Pitkanen, Yusof Rahman, et al.
JIMD Reports
|
November 18, 2017
Assessment of the Effect of Once Daily Nitisinone Therapy on 24-h Urinary Metadrenalines and 5-Hydroxyindole Acetic Acid Excretion in Patients with Alkaptonuria After 4 Weeks of Treatment
A S Davison, B Norman, A M Milan, et al.
JIMD Reports
|
November 22, 2017
Cardiopulmonary Exercise Testing Reflects Improved Exercise Capacity in Response to Treatment in Morquio A Patients: Results of a 52-Week Pilot Study of Two Different Doses of Elosulfase Alfa
Kenneth I Berger, Barbara K Burton, Gregory D Lewis, et al.
JIMD Reports
|
November 22, 2017
EPG5-Related Vici Syndrome: A Primary Defect of Autophagic Regulation with an Emerging Phenotype Overlapping with Mitochondrial Disorders
Shanti Balasubramaniam, Lisa G Riley, Anand Vasudevan, et al.
JIMD Reports
|
November 22, 2017
Severe Hyperammonemic Encephalopathy Requiring Dialysis Aggravated by Prolonged Fasting and Intermittent High Fat Load in a Ramadan Fasting Month in a Patient with CPTII Homozygous Mutation
P Phowthongkum, C Ittiwut, V Shotelersuk
JIMD Reports
|
September 10, 2017
Liver Failure as the Presentation of Ornithine Transcarbamylase Deficiency in a 13-Month-Old Female
Farrah Rajabi, Lance H Rodan, Maureen M Jonas, et al.
JIMD Reports
|
September 10, 2017
ALG13-CDG with Infantile Spasms in a Male Patient Due to a De Novo ALG13 Gene Mutation
Wienke H Galama, Sandra L J Verhaagen-van den Akker, Dirk J Lefeber, et al.
JIMD Reports
|
February 26, 2018
Normal Growth in PKU Patients Under Low-Protein Diet in a Single-Center Cross-Sectional Study
Jana Matic, Nina A Zeltner, Johannes Häberle
JIMD Reports
|
February 26, 2018
Mitochondrial Encephalopathy: First Portuguese Report of a VARS2 Causative Variant
Sandra Pereira, Mariana Adrião, Mafalda Sampaio, et al.
JIMD Reports
|
February 16, 2018
Secondary Hemophagocytic Syndrome Associated with COG6 Gene Defect: Report and Review
Nouf Althonaian, Abdulrahman Alsultan, Eva Morava, et al.
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of 127
Search research articles
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Showing results (141-150 of 1,270) with videos related to
Sort By:
Page
of 127
JIMD Reports
|
November 17, 2017
Three Cases of Hereditary Tyrosinaemia Type 1: Neuropsychiatric Outcomes and Brain Imaging Following Treatment with NTBC
Helen Walker, Mervi Pitkanen, Yusof Rahman, et al.
JIMD Reports
|
November 18, 2017
Assessment of the Effect of Once Daily Nitisinone Therapy on 24-h Urinary Metadrenalines and 5-Hydroxyindole Acetic Acid Excretion in Patients with Alkaptonuria After 4 Weeks of Treatment
A S Davison, B Norman, A M Milan, et al.
JIMD Reports
|
November 22, 2017
Cardiopulmonary Exercise Testing Reflects Improved Exercise Capacity in Response to Treatment in Morquio A Patients: Results of a 52-Week Pilot Study of Two Different Doses of Elosulfase Alfa
Kenneth I Berger, Barbara K Burton, Gregory D Lewis, et al.
JIMD Reports
|
November 22, 2017
EPG5-Related Vici Syndrome: A Primary Defect of Autophagic Regulation with an Emerging Phenotype Overlapping with Mitochondrial Disorders
Shanti Balasubramaniam, Lisa G Riley, Anand Vasudevan, et al.
JIMD Reports
|
November 22, 2017
Severe Hyperammonemic Encephalopathy Requiring Dialysis Aggravated by Prolonged Fasting and Intermittent High Fat Load in a Ramadan Fasting Month in a Patient with CPTII Homozygous Mutation
P Phowthongkum, C Ittiwut, V Shotelersuk
JIMD Reports
|
September 10, 2017
Liver Failure as the Presentation of Ornithine Transcarbamylase Deficiency in a 13-Month-Old Female
Farrah Rajabi, Lance H Rodan, Maureen M Jonas, et al.
JIMD Reports
|
September 10, 2017
ALG13-CDG with Infantile Spasms in a Male Patient Due to a De Novo ALG13 Gene Mutation
Wienke H Galama, Sandra L J Verhaagen-van den Akker, Dirk J Lefeber, et al.
JIMD Reports
|
February 26, 2018
Normal Growth in PKU Patients Under Low-Protein Diet in a Single-Center Cross-Sectional Study
Jana Matic, Nina A Zeltner, Johannes Häberle
JIMD Reports
|
February 26, 2018
Mitochondrial Encephalopathy: First Portuguese Report of a VARS2 Causative Variant
Sandra Pereira, Mariana Adrião, Mafalda Sampaio, et al.
JIMD Reports
|
February 16, 2018
Secondary Hemophagocytic Syndrome Associated with COG6 Gene Defect: Report and Review
Nouf Althonaian, Abdulrahman Alsultan, Eva Morava, et al.
Page
of 127