Search research articles
Contact Us
Filters
Showing results (271-280 of 1,270) with videos related to
Page
of 127
Sort By:
JIMD Reports
|
January 24, 2015
Long-term functional outcomes of children with hurler syndrome treated with unrelated umbilical cord blood transplantation
Hannah Y Coletti, Mieke Aldenhoven, Karina Yelin, et al.
JIMD Reports
|
October 13, 2018
A Novel Truncating FLAD1 Variant, Causing Multiple Acyl-CoA Dehydrogenase Deficiency (MADD) in an 8-Year-Old Boy
B Ryder, M Tolomeo, Z Nochi, et al.
JIMD Reports
|
October 13, 2018
Case of Neonatal Fatality from Neuromuscular Variant of Glycogen Storage Disease Type IV
Tavleen Sandhu, Michelle Polan, Zhongxin Yu, et al.
JIMD Reports
|
May 8, 2023
A second case of glutaminase hyperactivity: Expanding the phenotype with epilepsy
Lynne Rumping, Petra J W Pouwels, Nicole I Wolf, et al.
JIMD Reports
|
July 21, 2025
Late-Onset Multiple Acyl-CoA Dehydrogenase Deficiency (MADD): A Case Report With a Complex Biochemical Profile
Romain Penicaud, Jean-Baptiste Ferron, Xavier Valette, et al.
JIMD Reports
|
July 14, 2025
A Mild Juvenile Onset Canavan Disease With Atypical Clinical Presentation and MRI Brain Features
Preeya Rehsi, Ata Siddiqui, Rahul Singh, et al.
JIMD Reports
|
July 14, 2025
A Pilot Study of Bone Marrow Transplantation in a GALT-Null Rat Model of Classic Galactosemia
Shauna A Rasmussen, Madelyn M Seemiller, Ingrid Smith, et al.
JIMD Reports
|
July 14, 2025
Mitochondrial DNA Pathogenic Variant Prevalence in Primary Mitochondrial Disease Patients With African (L) Mitochondrial Genome Haplogroups
Surita Meldau, Elizabeth M McCormick, Ibrahim George-Sankoh, et al.
JIMD Reports
|
March 6, 2024
Clinical, biochemical and molecular characterization of a new case with <i>FDX2</i>-related mitochondrial disorder: Potential biomarkers and treatment options
Parith Wongkittichote, Cassandra Pantano, Miao He, et al.
JIMD Reports
|
March 6, 2024
Non-Hodgkin lymphoma in a kidney transplanted patient with methylmalonic acidemia: Metabolic susceptibility and the role of immunosuppression
Alberto B Burlina, Alessandro P Burlina, Renzo Mignani, et al.
Page
of 127
Search research articles
Search
Showing results (271-280 of 1,270) with videos related to
Sort By:
Page
of 127
JIMD Reports
|
January 24, 2015
Long-term functional outcomes of children with hurler syndrome treated with unrelated umbilical cord blood transplantation
Hannah Y Coletti, Mieke Aldenhoven, Karina Yelin, et al.
JIMD Reports
|
October 13, 2018
A Novel Truncating FLAD1 Variant, Causing Multiple Acyl-CoA Dehydrogenase Deficiency (MADD) in an 8-Year-Old Boy
B Ryder, M Tolomeo, Z Nochi, et al.
JIMD Reports
|
October 13, 2018
Case of Neonatal Fatality from Neuromuscular Variant of Glycogen Storage Disease Type IV
Tavleen Sandhu, Michelle Polan, Zhongxin Yu, et al.
JIMD Reports
|
May 8, 2023
A second case of glutaminase hyperactivity: Expanding the phenotype with epilepsy
Lynne Rumping, Petra J W Pouwels, Nicole I Wolf, et al.
JIMD Reports
|
July 21, 2025
Late-Onset Multiple Acyl-CoA Dehydrogenase Deficiency (MADD): A Case Report With a Complex Biochemical Profile
Romain Penicaud, Jean-Baptiste Ferron, Xavier Valette, et al.
JIMD Reports
|
July 14, 2025
A Mild Juvenile Onset Canavan Disease With Atypical Clinical Presentation and MRI Brain Features
Preeya Rehsi, Ata Siddiqui, Rahul Singh, et al.
JIMD Reports
|
July 14, 2025
A Pilot Study of Bone Marrow Transplantation in a GALT-Null Rat Model of Classic Galactosemia
Shauna A Rasmussen, Madelyn M Seemiller, Ingrid Smith, et al.
JIMD Reports
|
July 14, 2025
Mitochondrial DNA Pathogenic Variant Prevalence in Primary Mitochondrial Disease Patients With African (L) Mitochondrial Genome Haplogroups
Surita Meldau, Elizabeth M McCormick, Ibrahim George-Sankoh, et al.
JIMD Reports
|
March 6, 2024
Clinical, biochemical and molecular characterization of a new case with <i>FDX2</i>-related mitochondrial disorder: Potential biomarkers and treatment options
Parith Wongkittichote, Cassandra Pantano, Miao He, et al.
JIMD Reports
|
March 6, 2024
Non-Hodgkin lymphoma in a kidney transplanted patient with methylmalonic acidemia: Metabolic susceptibility and the role of immunosuppression
Alberto B Burlina, Alessandro P Burlina, Renzo Mignani, et al.
Page
of 127