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JIMD Reports
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July 30, 2016
Diaphragmatic Eventration in Sisters with Asparagine Synthetase Deficiency: A Novel Homozygous ASNS Mutation and Expanded Phenotype
Jun Sun, Angela J McGillivray, Jason Pinner, et al.
JIMD Reports
|
July 30, 2016
The Spectrum of PAH Mutations and Increase of Milder Forms of Phenylketonuria in Sweden During 1965-2014
Annika Ohlsson, Helene Bruhn, Anna Nordenström, et al.
JIMD Reports
|
February 14, 2025
2-[<sup>18</sup>F] FDG PET/CT in Rapid Late-Onset Multiple Acyl-CoA Dehydrogenase Deficiency: A Case Report
Astrid Høj, Sonja Holm-Yildiz, Thomas Krag, et al.
JIMD Reports
|
January 20, 2025
D,L-3-hydroxybutyrate in the treatment of glucose transporter 1 deficiency syndrome (Glut1DS)
Aya Amer, Kathryn Murrell, Liza Edmonds, et al.
JIMD Reports
|
January 20, 2025
Does p-lactate increase in patients with GSD1 after ingesting a meal with common-size sources of fructose and galactose? Observations from a prospective, non-blinded, crossover pilot study
Camilla Diana B Caroee, Allan M Lund
JIMD Reports
|
January 17, 2025
Phenotypic variability and the gender paradox in the R363C variant of Fabry disease
Alison C Leslie, Jeanine Jarnes, Alia Ahmed, et al.
JIMD Reports
|
December 26, 2024
Sleep quality in children with hepatic glycogen storage diseases, a prospective observational pilot study
Lucas Agnoletto, Moya Vandeleur, Mary White, et al.
JIMD Reports
|
November 15, 2024
Acid sphingomyelinase deficiency and Gaucher disease in adults: Similarities and differences in two macrophage storage disorders
Eline C B Eskes, Laura van Dussen, Johannes M F G Aerts, et al.
JIMD Reports
|
November 8, 2024
Enhanced differentiation between 3-hydroxyglutaric and 2-hydroxyglutaric acids facilitates diagnostic testing for glutaric aciduria type 1
Denis Cyr, Michel Boutin, Bruno Maranda, et al.
JIMD Reports
|
November 8, 2024
Disease burden among patients with Arginase 1 deficiency and their caregivers: A multinational, cross-sectional survey
Sara Olofsson, Sofia Löfvendahl, Julia Widén, et al.
Page
of 127
Search research articles
Search
Showing results (21-30 of 1,268) with videos related to
Sort By:
Page
of 127
JIMD Reports
|
July 30, 2016
Diaphragmatic Eventration in Sisters with Asparagine Synthetase Deficiency: A Novel Homozygous ASNS Mutation and Expanded Phenotype
Jun Sun, Angela J McGillivray, Jason Pinner, et al.
JIMD Reports
|
July 30, 2016
The Spectrum of PAH Mutations and Increase of Milder Forms of Phenylketonuria in Sweden During 1965-2014
Annika Ohlsson, Helene Bruhn, Anna Nordenström, et al.
JIMD Reports
|
February 14, 2025
2-[<sup>18</sup>F] FDG PET/CT in Rapid Late-Onset Multiple Acyl-CoA Dehydrogenase Deficiency: A Case Report
Astrid Høj, Sonja Holm-Yildiz, Thomas Krag, et al.
JIMD Reports
|
January 20, 2025
D,L-3-hydroxybutyrate in the treatment of glucose transporter 1 deficiency syndrome (Glut1DS)
Aya Amer, Kathryn Murrell, Liza Edmonds, et al.
JIMD Reports
|
January 20, 2025
Does p-lactate increase in patients with GSD1 after ingesting a meal with common-size sources of fructose and galactose? Observations from a prospective, non-blinded, crossover pilot study
Camilla Diana B Caroee, Allan M Lund
JIMD Reports
|
January 17, 2025
Phenotypic variability and the gender paradox in the R363C variant of Fabry disease
Alison C Leslie, Jeanine Jarnes, Alia Ahmed, et al.
JIMD Reports
|
December 26, 2024
Sleep quality in children with hepatic glycogen storage diseases, a prospective observational pilot study
Lucas Agnoletto, Moya Vandeleur, Mary White, et al.
JIMD Reports
|
November 15, 2024
Acid sphingomyelinase deficiency and Gaucher disease in adults: Similarities and differences in two macrophage storage disorders
Eline C B Eskes, Laura van Dussen, Johannes M F G Aerts, et al.
JIMD Reports
|
November 8, 2024
Enhanced differentiation between 3-hydroxyglutaric and 2-hydroxyglutaric acids facilitates diagnostic testing for glutaric aciduria type 1
Denis Cyr, Michel Boutin, Bruno Maranda, et al.
JIMD Reports
|
November 8, 2024
Disease burden among patients with Arginase 1 deficiency and their caregivers: A multinational, cross-sectional survey
Sara Olofsson, Sofia Löfvendahl, Julia Widén, et al.
Page
of 127