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JIMD Reports
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September 9, 2020
Chondroitin sulfate disaccharide is a specific and sensitive biomarker for mucopolysaccharidosis type IVA
Sharon J Chin, Jennifer T Saville, Belinda K McDermott, et al.
JIMD Reports
|
September 9, 2020
Mannose phosphate isomerase deficiency-congenital disorder of glycosylation (MPI-CDG) with cerebral venous sinus thrombosis as first and only presenting symptom: A rare but treatable cause of thrombophilia
Chris Mühlhausen, Lisa Henneke, Lars Schlotawa, et al.
JIMD Reports
|
November 20, 2019
Diagnostic pitfalls in vitamin B6-dependent epilepsy caused by mutations in the <i>PLPBP</i> gene
Kristian Vestergaard Jensen, Maria Frid, Tommy Stödberg, et al.
JIMD Reports
|
November 20, 2019
High diagnostic yield of direct Sanger sequencing in the diagnosis of neuronal ceroid lipofuscinoses
Abdulhakim Jilani, Diana Matviychuk, Susan Blaser, et al.
JIMD Reports
|
March 11, 2020
Pre-school neurocognitive and functional outcomes after liver transplant in children with early onset urea cycle disorders, maple syrup urine disease, and propionic acidemia: An inception cohort matched-comparison study
Shailly Jain-Ghai, Ari R Joffe, Gwen Y Bond, et al.
JIMD Reports
|
December 26, 2013
Mutations in the Complex III Assembly Factor Tetratricopeptide 19 Gene TTC19 Are a Rare Cause of Leigh Syndrome
P S Atwal
JIMD Reports
|
November 6, 2013
Influence of PAH Genotype on Sapropterin Response in PKU: Results of a Single-Center Cohort Study
Sarah Leuders, Eva Wolfgart, Torsten Ott, et al.
JIMD Reports
|
November 6, 2013
Evaluation of physiological amino acids profiling by tandem mass spectrometry
Romain Filee, Roland Schoos, François Boemer
JIMD Reports
|
November 7, 2013
Aminoglycoside-Induced Premature Stop Codon Read-Through of Mucopolysaccharidosis Type I Patient Q70X and W402X Mutations in Cultured Cells
Makoto Kamei, Karissa Kasperski, Maria Fuller, et al.
JIMD Reports
|
March 17, 2021
Low excretor glutaric aciduria type 1 of insidious onset with dystonia and atypical clinical features, a diagnostic dilemma
Jason Foran, Michael Moore, Ellen Crushell, et al.
Page
of 127
Search research articles
Search
Showing results (361-370 of 1,270) with videos related to
Sort By:
Page
of 127
JIMD Reports
|
September 9, 2020
Chondroitin sulfate disaccharide is a specific and sensitive biomarker for mucopolysaccharidosis type IVA
Sharon J Chin, Jennifer T Saville, Belinda K McDermott, et al.
JIMD Reports
|
September 9, 2020
Mannose phosphate isomerase deficiency-congenital disorder of glycosylation (MPI-CDG) with cerebral venous sinus thrombosis as first and only presenting symptom: A rare but treatable cause of thrombophilia
Chris Mühlhausen, Lisa Henneke, Lars Schlotawa, et al.
JIMD Reports
|
November 20, 2019
Diagnostic pitfalls in vitamin B6-dependent epilepsy caused by mutations in the <i>PLPBP</i> gene
Kristian Vestergaard Jensen, Maria Frid, Tommy Stödberg, et al.
JIMD Reports
|
November 20, 2019
High diagnostic yield of direct Sanger sequencing in the diagnosis of neuronal ceroid lipofuscinoses
Abdulhakim Jilani, Diana Matviychuk, Susan Blaser, et al.
JIMD Reports
|
March 11, 2020
Pre-school neurocognitive and functional outcomes after liver transplant in children with early onset urea cycle disorders, maple syrup urine disease, and propionic acidemia: An inception cohort matched-comparison study
Shailly Jain-Ghai, Ari R Joffe, Gwen Y Bond, et al.
JIMD Reports
|
December 26, 2013
Mutations in the Complex III Assembly Factor Tetratricopeptide 19 Gene TTC19 Are a Rare Cause of Leigh Syndrome
P S Atwal
JIMD Reports
|
November 6, 2013
Influence of PAH Genotype on Sapropterin Response in PKU: Results of a Single-Center Cohort Study
Sarah Leuders, Eva Wolfgart, Torsten Ott, et al.
JIMD Reports
|
November 6, 2013
Evaluation of physiological amino acids profiling by tandem mass spectrometry
Romain Filee, Roland Schoos, François Boemer
JIMD Reports
|
November 7, 2013
Aminoglycoside-Induced Premature Stop Codon Read-Through of Mucopolysaccharidosis Type I Patient Q70X and W402X Mutations in Cultured Cells
Makoto Kamei, Karissa Kasperski, Maria Fuller, et al.
JIMD Reports
|
March 17, 2021
Low excretor glutaric aciduria type 1 of insidious onset with dystonia and atypical clinical features, a diagnostic dilemma
Jason Foran, Michael Moore, Ellen Crushell, et al.
Page
of 127