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JIMD reports

Showing results (561-570 of 1,250) with videos related to

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JIMD Reports|July 1, 2015
Screening Mucopolysaccharidosis Type IX in Patients with Juvenile Idiopathic ArthritisErtugrul Kiykim, Kenan Barut, Mehmet Serif Cansever, et al.
JIMD Reports|May 27, 2015
CSF 5-Methyltetrahydrofolate Serial Monitoring to Guide Treatment of Congenital Folate Malabsorption Due to Proton-Coupled Folate Transporter (PCFT) DeficiencyA Torres, S A Newton, B Crompton, et al.
JIMD Reports|August 3, 2016
DMP1-CDG (CDG1e) with Significant Gastrointestinal Manifestations; Phenotype and Genotype ExpansionC Bursle, D Brown, J Cardinal, et al.
JIMD Reports|November 7, 2022
Alternative sources of valine and isoleucine for prompt reduction of plasma leucine in maple syrup urine disease patients: A case seriesMaryam Ziadlou, Anita MacDonald
JIMD Reports|November 7, 2022
MicroRNA and metabolomics signatures for adrenomyeloneuropathy disease severityBela Rui Turk, Laila Marie Poisson, Christina Linnea Nemeth, et al.
JIMD Reports|December 8, 2025
Course of Pregnancy in a Woman With Familial Chylomicronemia Syndrome Treated With Plozasiran, a Small Interfering RNA Against ApoC3Miriam Larouche, Diane Brisson, Nathalie Roy, et al.
JIMD Reports|January 21, 2026
Hypoaminoacidemia and Pyroglutamic Aciduria: Potential Biomarkers in Malnutrition-Related HyperammonemiaM M Crenshaw, O M D'Annibale, V Martucci, et al.
JIMD Reports|January 13, 2026
Liver Transplantation in PNPO Deficiency: Management Challenges and Biological LessonsRichard Webster, Bindu Parayil Sankaran, Sushil Bandodkar, et al.
JIMD Reports|December 29, 2025
Retrospective Case Series of Fulminant Metabolic Crisis in GSDIA: Persistent Lactic Acidosis Despite Correction of Hypoglycemia May Reflect Secondary Mitochondrial DysfunctionHerodes Guzman, Nicole Stewart, Lauren Mitteer, et al.
JIMD Reports|January 29, 2026
A Novel <i>PCK1</i> Gene Variant Associated With Cytosolic Phosphoenolpyruvate Carboxykinase Deficiency: Two Siblings With Different Clinical PresentationsLauma Vasiļevska, Ieva Puķīte, Madara Auzenbaha, et al.
Pageof 125

Showing results (561-570 of 1,250) with videos related to

Sort By:
Pageof 125
JIMD Reports|July 1, 2015
Screening Mucopolysaccharidosis Type IX in Patients with Juvenile Idiopathic ArthritisErtugrul Kiykim, Kenan Barut, Mehmet Serif Cansever, et al.
JIMD Reports|May 27, 2015
CSF 5-Methyltetrahydrofolate Serial Monitoring to Guide Treatment of Congenital Folate Malabsorption Due to Proton-Coupled Folate Transporter (PCFT) DeficiencyA Torres, S A Newton, B Crompton, et al.
JIMD Reports|August 3, 2016
DMP1-CDG (CDG1e) with Significant Gastrointestinal Manifestations; Phenotype and Genotype ExpansionC Bursle, D Brown, J Cardinal, et al.
JIMD Reports|November 7, 2022
Alternative sources of valine and isoleucine for prompt reduction of plasma leucine in maple syrup urine disease patients: A case seriesMaryam Ziadlou, Anita MacDonald
JIMD Reports|November 7, 2022
MicroRNA and metabolomics signatures for adrenomyeloneuropathy disease severityBela Rui Turk, Laila Marie Poisson, Christina Linnea Nemeth, et al.
JIMD Reports|December 8, 2025
Course of Pregnancy in a Woman With Familial Chylomicronemia Syndrome Treated With Plozasiran, a Small Interfering RNA Against ApoC3Miriam Larouche, Diane Brisson, Nathalie Roy, et al.
JIMD Reports|January 21, 2026
Hypoaminoacidemia and Pyroglutamic Aciduria: Potential Biomarkers in Malnutrition-Related HyperammonemiaM M Crenshaw, O M D'Annibale, V Martucci, et al.
JIMD Reports|January 13, 2026
Liver Transplantation in PNPO Deficiency: Management Challenges and Biological LessonsRichard Webster, Bindu Parayil Sankaran, Sushil Bandodkar, et al.
JIMD Reports|December 29, 2025
Retrospective Case Series of Fulminant Metabolic Crisis in GSDIA: Persistent Lactic Acidosis Despite Correction of Hypoglycemia May Reflect Secondary Mitochondrial DysfunctionHerodes Guzman, Nicole Stewart, Lauren Mitteer, et al.
JIMD Reports|January 29, 2026
A Novel <i>PCK1</i> Gene Variant Associated With Cytosolic Phosphoenolpyruvate Carboxykinase Deficiency: Two Siblings With Different Clinical PresentationsLauma Vasiļevska, Ieva Puķīte, Madara Auzenbaha, et al.
Pageof 125