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Molecular Therapy. Nucleic Acids|December 14, 2016
A Novel PD-L1-targeting Antagonistic DNA Aptamer With Antitumor EffectsWei-Yun Lai, Bo-Tsang Huang, Jen-Wei Wang, et al.Molecular Therapy. Nucleic Acids|November 30, 2016
Restoring Ureagenesis in Hepatocytes by CRISPR/Cas9-mediated Genomic Addition to Arginase-deficient Induced Pluripotent Stem CellsPatrick C Lee, Brian Truong, Agustin Vega-Crespo, et al.Molecular Therapy. Nucleic Acids|November 30, 2016
Efficient Generation of Orthologous Point Mutations in Pigs via CRISPR-assisted ssODN-mediated Homology-directed RepairKankan Wang, Xiaochun Tang, Yan Liu, et al.Molecular Therapy. Nucleic Acids|October 19, 2016
Activation of Fetal γ-globin Gene Expression via Direct Protein Delivery of Synthetic Zinc-finger DNA-Binding DomainsMir A Hossain, Yong Shen, Isaac Knudson, et al.Molecular Therapy. Nucleic Acids|September 28, 2016
Validation of RNAi Silencing Efficiency Using Gene Array Data shows 18.5% Failure Rate across 429 Independent ExperimentsGyöngyi Munkácsy, Zsófia Sztupinszki, Péter Herman, et al.Molecular Therapy. Nucleic Acids|March 23, 2017
Type I Interferons Impede Short Hairpin RNA-Mediated RNAi via Inhibition of Dicer-Mediated Processing to Small Interfering RNAMitsuhiro Machitani, Fuminori Sakurai, Keisaku Wakabayashi, et al.Molecular Therapy. Nucleic Acids|March 23, 2017
Aptamer-Drug Conjugates of Active Metabolites of Nucleoside Analogs and Cytotoxic Agents Inhibit Pancreatic Tumor Cell GrowthSorah Yoon, Kai-Wen Huang, Vikash Reebye, et al.Molecular Therapy. Nucleic Acids|May 1, 2014
RNAi-mediated Gene Silencing of Mutant Myotilin Improves Myopathy in LGMD1A MiceJian Liu, Lindsay M Wallace, Sara E Garwick-Coppens, et al.Molecular Therapy. Nucleic Acids|January 30, 2017
A Glu-urea-Lys Ligand-conjugated Lipid Nanoparticle/siRNA System Inhibits Androgen Receptor Expression In VivoJustin B Lee, Kaixin Zhang, Yuen Yi C Tam, et al.Molecular Therapy. Nucleic Acids|January 30, 2017
DNA Minicircle Technology Improves Purity of Adeno-associated Viral Vector PreparationsMaria Schnödt, Marco Schmeer, Barbara Kracher, et al.Pageof 308