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Molecular Therapy. Nucleic Acids|September 26, 2022
MicroRNA-dependent inhibition of WEE1 controls cancer stem-like characteristics and malignant behavior in ovarian cancerJin Gu Cho, Sung-Wook Kim, Aram Lee, et al.
Molecular Therapy. Nucleic Acids|February 6, 2014
Deep Sequencing Insights in Therapeutic shRNA Processing and siRNA Target Cleavage PrecisionHubert Denise, Sterghios A Moschos, Benjamin Sidders, et al.
Molecular Therapy. Nucleic Acids|January 29, 2025
Modeling and correction of protein conformational disease in iPSC-derived neurons through personalized base editingColin T Konishi, Nancy Mulaiese, Tanvi Butola, et al.
Molecular Therapy. Nucleic Acids|February 4, 2025
Gal-3 activates Tyro3 to ameliorate ferroptosis of hippocampal neurons after traumatic brain injuryXiao Zhang, Manrui Li, Yang Xu, et al.
Molecular Therapy. Nucleic Acids|February 3, 2025
miR-125b differentially impacts mineralization in dexamethasone and calcium-treated human mesenchymal stem cellsVirginie Joris, Elizabeth R Balmayor, Martijn van Griensven
Molecular Therapy. Nucleic Acids|January 15, 2025
Restoring hematopoietic stem and progenitor cell function in Fancc mice by in situ delivery of RNA lipid nanoparticlesOmar Banda, Sarah E Adams, Linah Omer, et al.
Molecular Therapy. Nucleic Acids|January 6, 2025
Specific inhibition of fibroblast growth factor receptor 1 signaling by a DNA aptamerVladimira Zlinska, Zuzana Feketova, Aleksandra Czyrek, et al.
Molecular Therapy. Nucleic Acids|January 6, 2025
uORF-targeting steric block antisense oligonucleotides do not reproducibly increase RNASEH1 expressionNina Ahlskog, Nenad Svrzikapa, Rushdie Abuhamdah, et al.
Molecular Therapy. Nucleic Acids|March 25, 2025
In vivo base editing of Angptl3 via lipid nanoparticles to treat cardiovascular diseaseJennifer Khirallah, Hanan Bloomer, Douglas Wich, et al.
Molecular Therapy. Nucleic Acids|March 24, 2025
Ligand-modified rAAV6 vectors with nanoblades allow high-level gene knockin in HSPCs without compromising cell survivalAlejandra Gutierrez-Guerrero, Séverine Périan, Aurélien Leray, et al.
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