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Lawrence Shoemaker

1PUBLICATIONS

7CO-AUTHORS

Gene and molecular therapy

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Publications (1)

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|Mar 19, 2026

Sirolimus for the treatment of steroid-refractory hepatotoxicity following AAV gene therapy in patients with Duchenne muscular dystrophy.

Carmen Leon-Astudillo, Stephanie M Salabarria, Christina B Chadwick

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Frequent Collaborators

1 joint publications

Carmen Leon-Astudillo

1 joint publications

Stephanie M Salabarria

1 joint publications

Christina B Chadwick

1 joint publications

Carla D Zingariello

1 joint publications

Julie Berthy

1 joint publications

Manuela Corti

1 joint publications

Barry J Byrne

Frequent Collaborators

1 joint publications

Carmen Leon-Astudillo

1 joint publications

Stephanie M Salabarria

1 joint publications

Christina B Chadwick

1 joint publications

Carla D Zingariello

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