Tippi C MacKenzie

10PUBLICATIONS
76CO-AUTHORS
Gene and molecular therapyApplied immunology (incl. antibody engineering, xenotransplantation and t-cell therapies)Solid tumoursInfant and child healthFoetal development and medicine
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Publications (10)

|Apr 27, 2026
Combinatorial base editing couples disease correction with lineage amplification in hematopoietic stem and progenitor cells.

|Apr 15, 2026
In utero hematopoietic cell transplantation in fetuses with α-thalassemia major: a phase 1 clinical trial.

|Aug 08, 2025
Integrated single-nuclei and spatial transcriptomic profiling of human sacrococcygeal teratomas reveals heterogeneity in cellular composition and X-chromosome inactivation.

Ernesto J Rojas, Krinio Giannikou, Benjamin J Huang

|May 14, 2025
Intra-amniotic antisense oligonucleotide treatment improves phenotypes in preclinical models of spinal muscular atrophy.

Beltran Borges, Stephen M Brown, Wan-Jin Chen

|Jul 11, 2024
In utero hematopoietic stem cell transplantation for Fanconi anemia.

Leah Swartzrock, Carla Dib, Morgane Denis

|May 20, 2024
Dual α-globin and truncated EPO receptor knockin restores hemoglobin production in α-thalassemia-derived red blood cells.

Simon N Chu, Eric Soupene, Beeke Wienert

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Frequent Collaborators

3 joint publications

Marco Cordero

2 joint publications

Michela Frascoli

2 joint publications

Russell Witt

2 joint publications

Simon N Chu