Oleksandr Platoshyn

1PUBLICATIONS
6CO-AUTHORS
Gene and molecular therapy
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Publications (1)

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|Sep 15, 2020
The sustained expression of Cas9 targeting toxic RNAs reverses disease phenotypes in mouse models of myotonic dystrophy type 1.

Ranjan Batra, David A Nelles, Daniela M Roth

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Frequent Collaborators

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Takahiro Tadokoro

1 joint publications

James D Thomas

1 joint publications

Łukasz J Sznajder

1 joint publications

Martin Marsala

1 joint publications

Maurice S Swanson

1 joint publications

Gene W Yeo

Frequent Collaborators

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Takahiro Tadokoro

1 joint publications

James D Thomas

1 joint publications

Łukasz J Sznajder

1 joint publications

Martin Marsala

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