Deborah Elstein
4PUBLICATIONS
10CO-AUTHORS
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Publications (4)
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|Jun 27, 2024
Twelve Years of the Gaucher Outcomes Survey (GOS): Insights, Achievements, and Lessons Learned from a Global Patient Registry.Deborah Elstein, Nadia Belmatoug, Bruno Bembi
|May 25, 2024
Long-Term Treatment of Gaucher Disease with Velaglucerase Alfa in ERT-Naïve Patients from the Gaucher Outcome Survey (GOS) Registry.Patrick Deegan, Heather Lau, Deborah Elstein
|Jul 21, 2023
A global neuronopathic gaucher disease registry (GARDIAN): a patient-led initiative.Tanya Collin-Histed, Madeline Stoodley, Kathleen Beusterien
|Jan 07, 2022
Development and validation of Gaucher disease type 1 (GD1)-specific patient-reported outcome measures (PROMs) for clinical monitoring and for clinical trials.Deborah Elstein, Nadia Belmatoug, Patrick Deegan
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Frequent Collaborators
2 joint publications
Patrick Deegan
2 joint publications
Heather Lau
2 joint publications
Pilar Giraldo
2 joint publications
Ari Zimran
2 joint publications
Majdolen Istaiti
2 joint publications
Shoshana Revel-Vilk
1 joint publications
Tanya Collin-Histed
1 joint publications
Kathleen Beusterien
1 joint publications
Nadia Belmatoug
1 joint publications
Özlem Göker-Alpan
