Hernan Gonorazky

8PUBLICATIONS
47CO-AUTHORS
Molecular medicinePharmacogenomicsNeonatologyFamily careNeurology and neuromuscular diseases
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Publications (8)

|May 15, 2026
Vamorolone Safety, Pharmacokinetics, and Exploratory Efficacy in Duchenne Muscular Dystrophy: A Phase II, Nonrandomized, Multiple-Dose Study in 2-<4-Year-Old Boys.

|Mar 03, 2026
Results of a phase II open-label, multiple-dose study of vamorolone (VBP15-006) in 7- to < 18-year-old boys with duchenne muscular dystrophy.

Hanns Lochmüller, Hernan Gonorazky, Elisa Nigro

|Dec 26, 2025
Pediatric Cohort of Charcot-Marie-Tooth Disease: Clinical Features and Genetic Distribution.

Issa Alawneh, Alberto Alemán, Elisa Nigro

|Sep 03, 2025
Disease-modifying therapies for spinal muscular atrophy: Family experience, ethical considerations, and the role of social determinants of health.

Lena Xiao, Djurdja Djordjevic, Sohee Kang

|Aug 27, 2024
Pediatric Chronic Inflammatory Demyelinating Polyneuropathy: Challenges in Diagnosis and Therapeutic Strategies.

Issa Alawneh, Asmaa Alenizi, Freddy Paiz

|Oct 04, 2022
Respiratory characteristics in children with spinal muscular atrophy type 1 receiving nusinersen.

Lena Xiao, Jackie Chiang, Maria Castro-Codesal

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Frequent Collaborators

3 joint publications

Elisa Nigro

3 joint publications

Alberto Alemán

2 joint publications

Lena Xiao

2 joint publications

Jackie Chiang