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Marshall Summar

4PUBLICATIONS

5CO-AUTHORS

Molecular targetsEpidemiological methodsProteins and peptidesDiagnostic radiography

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Publications (4)

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|May 08, 2026

Supply and Demand in the Mathematics of Rare Disease Drug Development: Why Choosing the Right Model Is Crucial.

|Apr 29, 2026

The Placebo Effect in Rare Disease Clinical Trials: Measurement, Impact, and Statistical Approaches for Patient-as-Own-Control Designs.

|Nov 25, 2024

Potential therapeutic uses of L-citrulline beyond genetic urea cycle disorders.

Marshall Summar

|May 23, 2022

The Rare Disease Research Scholars Program: A training curriculum for clinical researchers with mixed methods evaluation study.

Debra S Regier, Jennifer A Weaver, Nancy Cheng

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Frequent Collaborators

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Debra S Regier

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Jennifer A Weaver

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Mark L Batshaw

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Michael E Shy

Frequent Collaborators

1 joint publications

Debra S Regier

1 joint publications

Jennifer A Weaver

1 joint publications

Mark L Batshaw

1 joint publications

Mary Ottolini