Karl Eugen Mengel

7PUBLICATIONS
23CO-AUTHORS
German languageNeurology and neuromuscular diseasesAnimal growth and developmentCentral nervous system
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Publications (7)

|May 27, 2024
Qualitative Study of the Patient Experience with Venglustat for Gaucher Disease Type 3 in a Phase 2 Open-Label, Multicenter, Multinational Study (LEAP).

Raphael Schiffmann, Eugen Mengel, Mary Wallace

|Jan 31, 2024
Trial of N-Acetyl-l-Leucine in Niemann-Pick Disease Type C.

Tatiana Bremova-Ertl, Uma Ramaswami, Marion Brands

|Oct 18, 2022
Venglustat combined with imiglucerase for neurological disease in adults with Gaucher disease type 3: the LEAP trial.

Raphael Schiffmann, Timothy M Cox, Jean-François Dedieu

|May 26, 2022
Long-term Safety and Efficacy of Avalglucosidase Alfa in Patients With Late-Onset Pompe Disease.

Mazen M Dimachkie, Richard J Barohn, Barry Byrne

|Aug 21, 2021
Efficacy and safety of arimoclomol in Niemann-Pick disease type C: Results from a double-blind, randomised, placebo-controlled, multinational phase 2/3 trial of a novel treatment.

Eugen Mengel, Marc C Patterson, Rosalia M Da Riol

|Jun 02, 2021
Correction to: Clinical disease progression and biomarkers in Niemann-Pick disease type C: a prospective cohort study.

Eugen Mengel, Bruno Bembi, Mireia Del Toro

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Frequent Collaborators

2 joint publications

Raphael Schiffmann

1 joint publications

Timothy M Cox

1 joint publications

Tatiana Bremova-Ertl

1 joint publications

Uma Ramaswami