Mandana Arbab

2PUBLICATIONS
22CO-AUTHORS
Neurology and neuromuscular diseasesRegenerative medicine (incl. stem cells)
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Publications (2)

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|May 26, 2025
Base editing of trinucleotide repeats that cause Huntington's disease and Friedreich's ataxia reduces somatic repeat expansions in patient cells and in mice.

Zaneta Matuszek, Mandana Arbab, Maheswaran Kesavan

|Mar 30, 2023
Base editing rescue of spinal muscular atrophy in cells and in mice.

Mandana Arbab, Zaneta Matuszek, Kaitlyn M Kray

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Frequent Collaborators

2 joint publications

Zaneta Matuszek

2 joint publications

David R Liu

2 joint publications

Guangping Gao

1 joint publications

Kaitlyn M Kray

1 joint publications

Ailing Du

1 joint publications

Gregory A Newby

1 joint publications

Anton J Blatnik

1 joint publications

Aditya Raguram

1 joint publications

Ricardo Mouro Pinto

1 joint publications

Kevin T Zhao

Frequent Collaborators

2 joint publications

Zaneta Matuszek

2 joint publications

David R Liu

2 joint publications

Guangping Gao

1 joint publications

Kaitlyn M Kray

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