Efrain Sanchez-Ortiz

9PUBLICATIONS
41CO-AUTHORS
Regenerative medicine (incl. stem cells)Cardiology (incl. cardiovascular diseases)Microelectromechanical systems (MEMS)Medical devicesReaction engineering (excl. nuclear reactions)
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Publications (9)

|May 18, 2026
A human cardiomyocyte screen identifies optimized lipid nanoparticles for in vivo cardiac gene editing.

|Feb 20, 2026
Ablation of PKCα Phosphorylation by CRISPR-Cas9 Base Editing Rescues Heart Failure.

Tomonori Tadokoro, Hui Li, Peiheng Gan

|May 16, 2025
Genomic Editing of a Pathogenic Sequence Variant in ACTA2 Rescues Multisystemic Smooth Muscle Dysfunction Syndrome in Mice.

Qianqian Ding, Peiheng Gan, Zhisheng Xu

|Nov 23, 2022
Precise genomic editing of pathogenic mutations in RBM20 rescues dilated cardiomyopathy.

Takahiko Nishiyama, Yu Zhang, Miao Cui

|May 01, 2021
Precise correction of Duchenne muscular dystrophy exon deletion mutations by base and prime editing.

F Chemello, A C Chai, H Li

|Mar 05, 2020
Enhanced CRISPR-Cas9 correction of Duchenne muscular dystrophy in mice by a self-complementary AAV delivery system.

Yu Zhang, Hui Li, Yi-Li Min

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Frequent Collaborators

9 joint publications

Eric N Olson

8 joint publications

Hui Li

5 joint publications

Rhonda Bassel-Duby

4 joint publications

Wei Tan