Nina Raben

5PUBLICATIONS
11CO-AUTHORS
PharmacogenomicsMechanobiologyReaction engineering (excl. nuclear reactions)Medical molecular engineering of nucleic acids and proteinsGene and molecular therapy
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Publications (5)

|Jan 16, 2025
Expanding therapeutic options for Pompe disease: a new small molecule inhibitor of glycogen synthase 1 (GYS1) shows preclinical promise in Pompe disease.

Rebecca L Koch, Benjamin T Cocanougher, Jeong-A Lim

|Mar 06, 2024
Intravital imaging of muscle damage and response to therapy in a model of Pompe disease.

Naresh K Meena, Yeap Ng, Davide Randazzo

|Oct 04, 2021
Chemoenzymatic glycan-selective remodeling of a therapeutic lysosomal enzyme with high-affinity M6P-glycan ligands. Enzyme substrate specificity is the name of the game.

Xiao Zhang, Huiying Liu, Naresh Meena

|Aug 18, 2018
Pompe Disease: From Basic Science to Therapy.

Lara Kohler, Rosa Puertollano, Nina Raben

|Jan 29, 2017
Modulation of mTOR signaling as a strategy for the treatment of Pompe disease.

Jeong-A Lim, Lishu Li, Orian S Shirihai

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Frequent Collaborators

1 joint publications

Lishu Li

1 joint publications

Orian S Shirihai

1 joint publications

Rosa Puertollano

1 joint publications

Xiao Zhang