Rita Ferla

2PUBLICATIONS
23CO-AUTHORS
Gene and molecular therapy
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Publications (2)

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|Mar 26, 2025
Retinal gene therapy for Stargardt disease with dual AAV intein vectors is both safe and effective in large animal models.

Rita Ferla, Eugenio Pugni, Mariangela Lupo

|Apr 13, 2022
Therapeutic homology-independent targeted integration in retina and liver.

Patrizia Tornabene, Rita Ferla, Manel Llado-Santaeularia

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Frequent Collaborators

2 joint publications

Alberto Auricchio

1 joint publications

Manel Llado-Santaeularia

1 joint publications

Margherita Dell'Anno

1 joint publications

Federica Esposito

1 joint publications

Emanuela Pone

1 joint publications

Hristiana Lyubenova

1 joint publications

Giulio Piluso

1 joint publications

Francesco Musacchia

1 joint publications

Mariangela Lupo

1 joint publications

Paola Tiberi

Frequent Collaborators

2 joint publications

Alberto Auricchio

1 joint publications

Manel Llado-Santaeularia

1 joint publications

Margherita Dell'Anno

1 joint publications

Federica Esposito

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