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Anil Chekuri

6PUBLICATIONS
14CO-AUTHORS
Optical technologyAutomotive combustion and fuel engineeringNeurogeneticsMedical molecular engineering of nucleic acids and proteins
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Journal

Publications (6)

Sort by Publication Date:
|Jan 16, 2026
ELP1 Gene Augmentation Restores Visual Function in a Mouse Model of Familial Dysautonomia.

Hui-Chen Cheng, Swanand Koli, Kate Lewis

|Sep 02, 2025
AAV2-mediated intravitreal delivery of exon-specific U1 snRNA rescues optic neuropathy in a mouse model of familial dysautonomia.

Anil Chekuri, Krishnakanth Kondabolu, Emily G Kirchner

|Dec 09, 2024
Engineered CRISPR-Base Editors as a Permanent Treatment for Familial Dysautonomia.

Shuqi Yun, Anil Chekuri, Jennifer Art

|Dec 15, 2021
Selective retinal ganglion cell loss and optic neuropathy in a humanized mouse model of familial dysautonomia.

Anil Chekuri, Emily M Logan, Aram J Krauson

|Jun 08, 2021
A deep learning approach to identify gene targets of a therapeutic for human splicing disorders.

Dadi Gao, Elisabetta Morini, Monica Salani

|Aug 07, 2019
Late-onset retinal degeneration pathology due to mutations in CTRP5 is mediated through HTRA1.

Anil Chekuri, Katarzyna Zientara-Rytter, Angel Soto-Hermida

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Frequent Collaborators

2 joint publications

Dadi Gao

2 joint publications

Elisabetta Morini

1 joint publications

Katarzyna Zientara-Rytter

1 joint publications

Suresh Subramani

1 joint publications

Radha Ayyagari

1 joint publications

Aram J Krauson

1 joint publications

Serkan Erdin

1 joint publications

William D Paquette

1 joint publications

Garry R Cutting

1 joint publications

Susan A Slaugenhaupt

Frequent Collaborators

2 joint publications

Dadi Gao

2 joint publications

Elisabetta Morini

1 joint publications

Katarzyna Zientara-Rytter

1 joint publications

Suresh Subramani

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