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Elizabeth M Simpson

11PUBLICATIONS

27CO-AUTHORS

Gene and molecular therapyEpigenetics (incl. genome methylation and epigenomics)Biomechanical engineeringMedical devicesHaematological tumours

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Publications (11)

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|Mar 09, 2026

First pilot study of intravenous rAAV-PAX6 gene therapy increases retinal-ganglion-cell-layer thickness and Notch1 transcription in a mouse model of aniridia.

Diana Djaksigulova, Sif G Kaad, Andrea J Korecki

|Feb 18, 2025

Minimally Humanized <i>Ezh2</i> Exon-18 Mouse Cell Lines Validate Preclinical CRISPR/Cas9 Approach to Treat Weaver Syndrome.

William T Gibson, Tess C Lengyell, Andrea J Korecki

|May 28, 2024

Taf1 knockout is lethal in embryonic male mice and heterozygous females show weight and movement disorders.

Elisa M Crombie, Andrea J Korecki, Karen Cleverley

|May 20, 2023

ABE8e Corrects Pax6-Aniridic Variant in Humanized Mouse ESCs and via LNPs in Ex Vivo Cortical Neurons.

Bethany A Adair, Andrea J Korecki, Diana Djaksigulova

|Apr 18, 2023

rAAV-PHP.B escapes the mouse eye and causes lethality whereas rAAV9 can transduce aniridic corneal limbal stem cells without lethality.

Seyedeh Zeinab Mirjalili Mohanna, Andrea J Korecki, Elizabeth M Simpson

|Feb 13, 2023

Sonoselective delivery using ultrasound and microbubbles combined with intravenous rAAV9 CLDN5-GFP does not increase endothelial gene expression.

Rikke Hahn Kofoed, Elizabeth M Simpson, Kullervo Hynynen

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Frequent Collaborators

4 joint publications

Jack W Hickmott

3 joint publications

Andrea J Korecki

2 joint publications

Tess C Lengyell

1 joint publications

Anthony Mathelier

1 joint publications

Russell J Bonaguro

1 joint publications

Daniel Goldowitz

1 joint publications

Jan M Deussing

1 joint publications

Wyeth W Wasserman

1 joint publications

Siu Ling Lam

1 joint publications

Oriol Fornes

Frequent Collaborators

4 joint publications

Jack W Hickmott

3 joint publications

Andrea J Korecki

2 joint publications

Tess C Lengyell

1 joint publications

Anthony Mathelier

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