Shunji Tomatsu
37PUBLICATIONS
64CO-AUTHORS

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Publications (37)
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|May 17, 2026
Natural History of Morquio A Syndrome.|Mar 14, 2026
AAV Gene Therapy for MPS IVA with Induction of Immune Tolerance via Oral Administration of Epitope Peptides of N-Acetylgalactosamine-6-sulfate Sulfatase.Sampurna Saikia, Yasuhiko Ago, Fnu Nidhi
|Jan 30, 2026
Collagen Type II-Targeting Lentiviral Gene Therapy for Mucopolysaccharidosis IVA.Betul Celik, Sampurna Saikia, Shaukat Khan
|Nov 26, 2025
Long-Term Liver-Targeted AAV8 Gene Therapy for Mucopolysaccharidosis IVA.Shaukat A Khan, Eliana Benincore-Florez, Fnu Nidhi
|Oct 01, 2025
Three-dimensional human mucopolysaccharidosis IVA chondrocyte culture reveals significant impairments in the lysosomal-mitochondrial crosstalk.Andrés Felipe Leal, Sampurna Saikia, Shaukat A Khan
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Frequent Collaborators
9 joint publications
Andrés Felipe Leal
8 joint publications
Betul Çelik
5 joint publications
Yasuhiko Ago
4 joint publications
Shaukat Khan
3 joint publications
Nidhi Fnu
3 joint publications
Susana B Bravo
3 joint publications
Cristóbal Colón
3 joint publications
Estera Rintz
3 joint publications
Francisco J Otero-Espinar
3 joint publications
Carlos Javier Alméciga-Díaz