Margarida Duarte Amaral

27PUBLICATIONS
42CO-AUTHORS
Gene and molecular therapyCancer geneticsCarbon capture engineering (excl. sequestration)Fluid-structure interaction and aeroacousticsCancer diagnosis
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Publications (27)

|Sep 13, 2025
Personalized Medicine in Cystic Fibrosis: Characterization of Eight Rare CFTR Variants in Intestinal Organoids and Cellular Models.

Violeta Railean, Cláudia S Rodrigues, Ines Pankonien

|Jun 27, 2025
Cystic fibrosis as a paradigmatic disease in bringing science to the bedside.

Margarida D Amaral, Ines Pankonien

|Jan 21, 2023
What Can RNA-Based Therapy Do for Monogenic Diseases?

Luka A Clarke, Margarida D Amaral

|Jan 21, 2023
Additive Potentiation of R334W-CFTR Function by Novel Small Molecules.

Mafalda Bacalhau, Filipa C Ferreira, Iris A L Silva

|Oct 27, 2022
Drug Repurposing for Cystic Fibrosis: Identification of Drugs That Induce CFTR-Independent Fluid Secretion in Nasal Organoids.

Lisa W Rodenburg, Livia Delpiano, Violeta Railean

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