Christiano R R Alves

19PUBLICATIONS
47CO-AUTHORS
Peripheral nervous systemNeurology and neuromuscular diseasesGene and molecular therapyEnvironmental biogeochemistryAutomotive combustion and fuel engineering
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Publications (19)

|Jul 17, 2026
Profiling circulating Tau and phospho-Tau isoforms in pediatric and adult spinal muscular atrophy identifies selective elevation of pTau-262 in adults.

|Apr 03, 2026
Cardiac defects in spinal muscular atrophy and the role of SMN in cardiomyocyte homeostasis.

Reid Garner, Leillani L Ha, Flavia C Nery

|Sep 11, 2025
Treatment of a severe vascular disease using a bespoke CRISPR-Cas9 base editor in mice.

Christiano R R Alves, Sabyasachi Das, Vijai Krishnan

|Jul 16, 2025
Poison exon splicing in the human brain: a new paradigm for understanding and targeting neurological disorders.

Paolo Pigini, Huilin Xu, Yan Ji

|Apr 01, 2025
Early life safety profiling of gene therapy for spinal muscular atrophy.

Rebecca G Spellman, Leillani L Ha, Salomé Da Silva Duarte Lepez

|Dec 09, 2024
Engineered CRISPR-Base Editors as a Permanent Treatment for Familial Dysautonomia.

Shuqi Yun, Anil Chekuri, Jennifer Art

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Frequent Collaborators

4 joint publications

Leillani L Ha

4 joint publications

Benjamin P Kleinstiver

4 joint publications

Kathryn J Swoboda

3 joint publications

Shengdar Q Tsai