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Christiano R R Alves

18PUBLICATIONS

47CO-AUTHORS

Neurology and neuromuscular diseasesGene and molecular therapyEnvironmental biogeochemistryAutomotive combustion and fuel engineeringPredictive and prognostic markers

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Publications (18)

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|Apr 03, 2026

Cardiac defects in spinal muscular atrophy and the role of SMN in cardiomyocyte homeostasis.

Reid Garner, Leillani L Ha, Flavia C Nery

|Sep 11, 2025

Treatment of a severe vascular disease using a bespoke CRISPR-Cas9 base editor in mice.

Christiano R R Alves, Sabyasachi Das, Vijai Krishnan

|Jul 16, 2025

Poison exon splicing in the human brain: a new paradigm for understanding and targeting neurological disorders.

Paolo Pigini, Huilin Xu, Yan Ji

|Apr 01, 2025

Early life safety profiling of gene therapy for spinal muscular atrophy.

Rebecca G Spellman, Leillani L Ha, Salomé Da Silva Duarte Lepez

|Dec 09, 2024

Engineered CRISPR-Base Editors as a Permanent Treatment for Familial Dysautonomia.

Shuqi Yun, Anil Chekuri, Jennifer Art

|Nov 28, 2024

<i>In vivo</i> Treatment of a Severe Vascular Disease via a Bespoke CRISPR-Cas9 Base Editor.

Christiano R R Alves, Sabyasachi Das, Vijai Krishnan

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Frequent Collaborators

4 joint publications

Leillani L Ha

4 joint publications

Benjamin P Kleinstiver

4 joint publications

Kathryn J Swoboda

3 joint publications

Shengdar Q Tsai

3 joint publications

Rashmi Kothary

2 joint publications

David Y Chung

2 joint publications

Shuqi Yun

2 joint publications

Rajeev Malhotra

2 joint publications

Eric J Eichelberger

2 joint publications

Salomé Da Silva Duarte Lepez

Frequent Collaborators

4 joint publications

Leillani L Ha

4 joint publications

Benjamin P Kleinstiver

4 joint publications

Kathryn J Swoboda

3 joint publications

Shengdar Q Tsai

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